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NCT05033080 · ClinicalTrials.gov registry record · Phase 3

A Phase 3 Study of VX-121 Combination Therapy in Participants With Cystic Fibrosis (CF) Heterozygous for F508del and a Minimal Function Mutation (F/MF)

A Phase 3 study, sponsored by Vertex Pharmaceuticals Incorporated.

Completed
Registry status
Phase 3
Development phase
435
Enrollment target

NCT05033080: Completed Phase 3 study, sponsored by Vertex Pharmaceuticals Incorporated.

NCT05033080 is a Phase 3 study that has completed, run by Vertex Pharmaceuticals Incorporated. The registered enrollment target is 435 participants, below the 772-participant average among 15,282 other Phase 3 trials with a reported enrollment target (44% lower). According to ClinicalTrials.gov, the official US trial registry.

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The verdict

NCT05033080, a Phase 3 study, has completed, sponsored by Vertex Pharmaceuticals Incorporated.

COMPLETED
Registry status
Phase 3
Development phase
435 participants
Enrollment target

Study Summary

The purpose of this study evaluates the efficacy and safety of VX-121/tezacaftor/deutivacaftor (VX-121/TEZ/D-IVA) in CF participants who were heterozygous for F508del and a minimal function mutation (F/MF participants).

Primary Outcome

FEV1 is the volume of air that can forcibly be blown out in one second, after full inspiration.

Interventions

  • DRUG VX-121/TEZ/D-IVA
  • DRUG IVA
  • DRUG ELX/TEZ/IVA
  • DRUG Placebo (matched to VX-121/TEZ/D-IVA)
  • DRUG Placebo (matched to ELX/TEZ/IVA)

Trial Details

FieldValue
Enrollment Target 435 participants
Start Date 2021-09-14
Est. Completion 2023-11-21
Phase Phase 3
Vertex Pharmaceuticals Incorporated

191 total trials

What the finished NCT05033080 record still lists

NCT05033080 is an interventional study that assigns participants to a tested intervention. The registered 435 participants enrollment target is mid-sized for trials with a published cap, below the 772-participant average among 15,282 other Phase 3 trials with a reported enrollment target (44% lower).

The record links to 0 conditions, and to 5 interventions - of which VX-121/TEZ/D-IVA is the first listed.

NCT05033080 does not publish any study locations in the registry export this page uses.

Frequently Asked Questions

What is clinical trial NCT05033080 about?

NCT05033080 is a clinical study titled "A Phase 3 Study of VX-121 Combination Therapy in Participants With Cystic Fibrosis (CF) Heterozygous for F508del and a Minimal Function Mutation (F/MF)". The purpose of this study evaluates the efficacy and safety of VX-121/tezacaftor/deutivacaftor (VX-121/TEZ/D-IVA) in CF participants who were heterozygous for F508del and a minimal function mutation (F/MF participants).

What is the current status of trial NCT05033080?

This trial is currently completed. It is a Phase 3 study. The enrollment target is 435 participants. The study started on 2021-09-14. Estimated completion is 2023-11-21.

What interventions are being tested in trial NCT05033080?

The interventions under investigation include: VX-121/TEZ/D-IVA (DRUG), IVA (DRUG), ELX/TEZ/IVA (DRUG), Placebo (matched to VX-121/TEZ/D-IVA) (DRUG), Placebo (matched to ELX/TEZ/IVA) (DRUG).

Who is sponsoring clinical trial NCT05033080?

This trial is sponsored by Vertex Pharmaceuticals Incorporated, which has 191 total clinical trials registered on ClinicalTrials.gov.

How this trial's enrollment target compares

Where NCT05033080's enrollment target sits among peer trials

435 875th of 2000 higher than 1,125 of 2,000 other Phase 3 trials

participants (enrollment target), bucketed by value

Each bar is a band; taller bars hold more other Phase 3 trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.

Source ClinicalTrials.gov registry export · 2026-08-08

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Source: ClinicalTrials.gov NCT05033080, the US trial registry maintained by the National Library of Medicine. NCT05033080 (mid enrollment · none site footprint · completed) retrieved and formatted by PlainTrial, see methodology.