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NCT04644549 · ClinicalTrials.gov registry record

Natural History Study of Batten Disease

A clinical trial, sponsored by Emily de los Reyes.

Terminated
Registry status
10
Enrollment target

NCT04644549: Clinical Trial study, sponsored by Emily de los Reyes.

NCT04644549 is a clinical trial that was terminated before completion, run by Emily de los Reyes. The registered enrollment target is 10 participants. According to ClinicalTrials.gov, the official US trial registry.

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The verdict

NCT04644549 was terminated before completion, sponsored by Emily de los Reyes.

TERMINATED
Registry status
10 participants
Enrollment target

Study Summary

This is a multicenter, international, study to assess the natural history data from people with Batten disease by collecting both retrospective and prospective information about the motor, behavioral and functional capabilities of patients. The study initially has 2 cohorts. Cohort 1 (n ≈ 75) includes subjects with CLN6 Batten disease. Cohort 2 (n ≈ 120) includes subjects with juvenile CLN3 Batten disease. Additional cohorts for other Batten disease subtypes may be added in the future.

Primary Outcome

The UBDRS is a clinical ratings instrument used specifically to assess motor, seizure, behavioral and functional capabilities.

Trial Details

FieldValue
Enrollment Target 10 participants
Start Date 2021-04-27
Est. Completion 2022-03-11
Emily de los Reyes

4 total trials

Why NCT04644549 stopped before completion

NCT04644549 is an observational study that tracks outcomes without assigning an intervention. The registry caps enrollment at 10 participants, a relatively small participant target.

The record links to 0 conditions, and to 0 interventions.

NCT04644549 does not publish any study locations in the registry export this page uses.

Frequently Asked Questions

What is clinical trial NCT04644549 about?

NCT04644549 is a clinical study titled "Natural History Study of Batten Disease". This is a multicenter, international, study to assess the natural history data from people with Batten disease by collecting both retrospective and prospective information about the motor, behavioral and functional capabilities of patients. The study initially has 2 cohorts. Cohort 1 (n ≈ 75) includ...

What is the current status of trial NCT04644549?

This trial is currently terminated. The enrollment target is 10 participants. The study started on 2021-04-27. Estimated completion is 2022-03-11.

Who is sponsoring clinical trial NCT04644549?

This trial is sponsored by Emily de los Reyes, which has 4 total clinical trials registered on ClinicalTrials.gov.

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Source: ClinicalTrials.gov NCT04644549, the US trial registry maintained by the National Library of Medicine. NCT04644549 (small enrollment · none site footprint · terminated) retrieved and formatted by PlainTrial, see methodology.