Medical Information Only. Always consult your healthcare provider before enrolling in any clinical trial.
NCT04644549 · ClinicalTrials.gov registry record
Natural History Study of Batten Disease
A clinical trial, sponsored by Emily de los Reyes.
- Terminated
- Registry status
- 10
- Enrollment target
NCT04644549: Clinical Trial study, sponsored by Emily de los Reyes.
NCT04644549 is a clinical trial that was terminated before completion, run by Emily de los Reyes. The registered enrollment target is 10 participants. According to ClinicalTrials.gov, the official US trial registry.
The verdict
NCT04644549 was terminated before completion, sponsored by Emily de los Reyes.
- TERMINATED
- Registry status
- 10 participants
- Enrollment target
Study Summary
This is a multicenter, international, study to assess the natural history data from people with Batten disease by collecting both retrospective and prospective information about the motor, behavioral and functional capabilities of patients. The study initially has 2 cohorts. Cohort 1 (n ≈ 75) includes subjects with CLN6 Batten disease. Cohort 2 (n ≈ 120) includes subjects with juvenile CLN3 Batten disease. Additional cohorts for other Batten disease subtypes may be added in the future.
Primary Outcome
The UBDRS is a clinical ratings instrument used specifically to assess motor, seizure, behavioral and functional capabilities.
Trial Details
| Field | Value |
|---|---|
| Enrollment Target | 10 participants |
| Start Date | 2021-04-27 |
| Est. Completion | 2022-03-11 |
Why NCT04644549 stopped before completion
NCT04644549 is an observational study that tracks outcomes without assigning an intervention. The registry caps enrollment at 10 participants, a relatively small participant target.
The record links to 0 conditions, and to 0 interventions.
NCT04644549 does not publish any study locations in the registry export this page uses.
Frequently Asked Questions
What is clinical trial NCT04644549 about?
NCT04644549 is a clinical study titled "Natural History Study of Batten Disease". This is a multicenter, international, study to assess the natural history data from people with Batten disease by collecting both retrospective and prospective information about the motor, behavioral and functional capabilities of patients. The study initially has 2 cohorts. Cohort 1 (n ≈ 75) includ...
What is the current status of trial NCT04644549?
This trial is currently terminated. The enrollment target is 10 participants. The study started on 2021-04-27. Estimated completion is 2022-03-11.
Who is sponsoring clinical trial NCT04644549?
This trial is sponsored by Emily de los Reyes, which has 4 total clinical trials registered on ClinicalTrials.gov.
Learn More About Clinical Trials
Nationwide trials with similar profiles
Cross-condition peers matched on enrollment target and registry start date, not the same-condition list above.
Similar enrollment target
- NCT00623389 · 10 participants · NA
Evaluation of an Advanced Lower Extremity Neuroprostheses
- NCT01241864 · 10 participants · Phase 2
Islet Transplantation in Type 1 Diabetic Kidney Allograft
- NCT01293214 · 10 participants · NA
Vascularized Composite Allotransplantation for Multiple Extremity Amputations
- NCT01474148 · 10 participants · NA
A Neuroprosthesis for Seated Posture and Balance
Similar registry start date
- NCT05962346 · started 2026-12 · NA
Fetal Endoscopic Tracheal Occlusion for Congenital Diaphragmatic Hernia
- NCT07125183 · started 2026-12 · Phase 2
Study on Efficacy and Tolerability of Weekly Doxorubicin in Elderly Patients With Advanced or Metastatic Leiomyosarcoma
- NCT07292298 · started 2026-11 · Phase 2
Phase 2 Single-Arm Rectal Cancer Brachytherapy for Patients With Low-Lying Residual Adenocarcinoma After Total Neoadjuvant Therapy to Improve Organ Preservation Rates
- NCT04263285 · started 2026-10 · NA
Treatment of Depression Post-SCI