Medical Information Only. Always consult your healthcare provider before enrolling in any clinical trial.

NCT04388254 · ClinicalTrials.gov registry record · Phase 2

Simufilam (PTI-125), 100 mg, for Mild-to-moderate Alzheimer's Disease Patients

A Phase 2 study, sponsored by Cassava Sciences.

Completed
Registry status
Phase 2
Development phase
220
Enrollment target

NCT04388254: Completed Phase 2 study, sponsored by Cassava Sciences.

NCT04388254 is a Phase 2 study that has completed, run by Cassava Sciences. The registered enrollment target is 220 participants, above the 133-participant average among 30,622 other Phase 2 trials with a reported enrollment target (65% higher). According to ClinicalTrials.gov, the official US trial registry.

View on ClinicalTrials.gov ↗

View your shortlist →

The verdict

NCT04388254, a Phase 2 study, has completed, sponsored by Cassava Sciences.

COMPLETED
Registry status
Phase 2
Development phase
220 participants
Enrollment target

Study Summary

A two-year safety study of simufilam (PTI-125) 100 mg oral tablets twice daily for participants of the previous simufilam studies as wells as additional new mild-to-moderate Alzheimer's disease subjects for a total of 200 participants. All participants will receive simufilam 100 mg tablets twice daily for one year, followed by a 6-month randomized, double-blind period where subjects will either continue on active treatment or be switched to placebo. The study concludes with an additional 6-month open-label treatment period. Clinic visits are every month or month and a half in the first year, and every 3 months in the second year with an additional visit at Month 13. Cognition and neuropsychiatric symptoms are evaluated.

Primary Outcome

Alzheimer's Disease Assessment Scale-Cognitive Subscale 11-item: Change from baseline in cognition over the course of 24 months Possible range in score: 0-70; Subscales are summed; Higher values represent a more cognitively impaired participant Decrease in mean value represents improvement in cognition from one timepoint to the next.

Interventions

  • DRUG Placebo
  • DRUG Simufilam 100 mg oral tablet

Trial Details

FieldValue
Enrollment Target 220 participants
Start Date 2020-03-24
Est. Completion 2023-11-09
Phase Phase 2
Cassava Sciences

9 total trials

What the finished NCT04388254 record still lists

NCT04388254 is an interventional study that assigns participants to a tested intervention. The registered 220 participants enrollment target is mid-sized for trials with a published cap, above the 133-participant average among 30,622 other Phase 2 trials with a reported enrollment target (65% higher).

The record links to 0 conditions, and to 2 interventions - of which Placebo is the first listed.

NCT04388254 does not publish any study locations in the registry export this page uses.

Frequently Asked Questions

What is clinical trial NCT04388254 about?

NCT04388254 is a clinical study titled "Simufilam (PTI-125), 100 mg, for Mild-to-moderate Alzheimer's Disease Patients". A two-year safety study of simufilam (PTI-125) 100 mg oral tablets twice daily for participants of the previous simufilam studies as wells as additional new mild-to-moderate Alzheimer's disease subjects for a total of 200 participants. All participants will receive simufilam 100 mg tablets twice dai...

What is the current status of trial NCT04388254?

This trial is currently completed. It is a Phase 2 study. The enrollment target is 220 participants. The study started on 2020-03-24. Estimated completion is 2023-11-09.

What interventions are being tested in trial NCT04388254?

The interventions under investigation include: Placebo (DRUG), Simufilam 100 mg oral tablet (DRUG).

Who is sponsoring clinical trial NCT04388254?

This trial is sponsored by Cassava Sciences, which has 9 total clinical trials registered on ClinicalTrials.gov.

How this trial's enrollment target compares

Where NCT04388254's enrollment target sits among peer trials

220 275th of 2000 higher than 1,718 of 2,000 other Phase 2 trials

participants (enrollment target), bucketed by value

Each bar is a band; taller bars hold more other Phase 2 trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.

Source ClinicalTrials.gov registry export · 2026-08-08

Nationwide trials with similar profiles

Cross-condition peers matched on enrollment target and registry start date, not the same-condition list above.

Similar enrollment target

  • NCT00920972 · 220 participants · Phase 1

    Campath/Fludarabine/Melphalan Transplant Conditioning for Non-Malignant Diseases

  • NCT01851642 · 220 participants

    Lung Disease and Its Affect on the Work of White Blood Cells in the Lungs

  • NCT02582021 · 220 participants

    WISE CVD - Continuation (WISE HFpEF)

  • NCT04067830 · 220 participants · Phase 2

    Respiratory Muscle Training Before Surgery in Preventing Lung Complications in Patients With Stage I-IIIB Lung Cancer

Similar registry start date

  • NCT05962346 · started 2026-12 · NA

    Fetal Endoscopic Tracheal Occlusion for Congenital Diaphragmatic Hernia

  • NCT07125183 · started 2026-12 · Phase 2

    Study on Efficacy and Tolerability of Weekly Doxorubicin in Elderly Patients With Advanced or Metastatic Leiomyosarcoma

  • NCT07292298 · started 2026-11 · Phase 2

    Phase 2 Single-Arm Rectal Cancer Brachytherapy for Patients With Low-Lying Residual Adenocarcinoma After Total Neoadjuvant Therapy to Improve Organ Preservation Rates

  • NCT04263285 · started 2026-10 · NA

    Treatment of Depression Post-SCI

Source: ClinicalTrials.gov NCT04388254, the US trial registry maintained by the National Library of Medicine. NCT04388254 (mid enrollment · none site footprint · completed) retrieved and formatted by PlainTrial, see methodology.