Medical Information Only. Always consult your healthcare provider before enrolling in any clinical trial.
NCT04337684 · ClinicalTrials.gov registry record
Long Term Follow-up on Menkes Disease Patients
A clinical trial of Menkes Disease, sponsored by Sentynl Therapeutics.
- Active
- Registry status
- 50
- Enrollment target
- 1
- Study location
NCT04337684: Active study of Menkes Disease, sponsored by Sentynl Therapeutics.
NCT04337684 is a study of Menkes Disease that is active but no longer recruiting, run by Sentynl Therapeutics. The registered enrollment target is 50 participants. The trial reports 1 study location across 1 state. According to ClinicalTrials.gov, the official US trial registry.
The verdict
NCT04337684, a study of Menkes Disease, is active but no longer recruiting, sponsored by Sentynl Therapeutics.
- ACTIVE NOT RECRUITING
- Registry status
- 50 participants
- Enrollment target
- 1
- Study location
Study Summary
This study will collect long term follow-up data regarding overall survival and neurological parameters from patients previously identified and/or enrolled in Protocols 09-CH-0059 and 90-CH0149 and Historical Control data on Menkes disease patients.
Primary Outcome
The primary outcome measure will be overall survival.
Conditions Studied
Interventions
- DRUG Long Term Follow-Up
Study Locations (1)
California
- Sentynl Therapeutics - Solana Beach
Trial Details
| Field | Value |
|---|---|
| Enrollment Target | 50 participants |
| Start Date | 2019-12-01 |
| Est. Completion | 2026-08-31 |
What the registry record for NCT04337684 still lists
NCT04337684 is an observational study that tracks outcomes without assigning an intervention. The registry caps enrollment at 50 participants, a relatively small participant target.
The record links to 1 condition, with Menkes Disease appearing as the primary indexed condition, and to 1 intervention - of which Long Term Follow-Up is the first listed.
NCT04337684 reports a single indexed study location in California.
Frequently Asked Questions
What is clinical trial NCT04337684 about?
NCT04337684 is a clinical study titled "Long Term Follow-up on Menkes Disease Patients". This study will collect long term follow-up data regarding overall survival and neurological parameters from patients previously identified and/or enrolled in Protocols 09-CH-0059 and 90-CH0149 and Historical Control data on Menkes disease patients.
What is the current status of trial NCT04337684?
This trial is currently active not recruiting. The enrollment target is 50 participants. The study started on 2019-12-01. Estimated completion is 2026-08-31.
What conditions does trial NCT04337684 study?
This clinical trial studies the following conditions: Menkes Disease.
What interventions are being tested in trial NCT04337684?
The interventions under investigation include: Long Term Follow-Up (DRUG).
Who is sponsoring clinical trial NCT04337684?
This trial is sponsored by Sentynl Therapeutics, which has 1 total clinical trials registered on ClinicalTrials.gov.
Where is trial NCT04337684 being conducted?
This trial has 1 study location across California. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.
Learn More About Clinical Trials
Similar trials for Menkes Disease
Matched on the same primary condition, ranked to surface studies in the same phase first, then by recruiting status, no relevance scoring or editorial curation.
Nationwide trials with similar profiles
Cross-condition peers matched on enrollment target and registry start date, not the same-condition list above.
Similar enrollment target
- NCT00200889 · 50 participants · Early Phase 1
Mapping Auricular Vagus Nerve Circuitry
- NCT00409435 · 50 participants · Phase 2
A Study of Pyridostigmine in Postural Tachycardia Syndrome
- NCT01202305 · 50 participants
The Use of Lymph Node Biopsies to Support HIV Pathogenesis Studies
- NCT01225913 · 50 participants · Phase 4
Mechanism(s) of Airflow Limitation During Exacerbation of Asthma
Similar registry start date
- NCT05962346 · started 2026-12 · NA
Fetal Endoscopic Tracheal Occlusion for Congenital Diaphragmatic Hernia
- NCT07125183 · started 2026-12 · Phase 2
Study on Efficacy and Tolerability of Weekly Doxorubicin in Elderly Patients With Advanced or Metastatic Leiomyosarcoma
- NCT07292298 · started 2026-11 · Phase 2
Phase 2 Single-Arm Rectal Cancer Brachytherapy for Patients With Low-Lying Residual Adenocarcinoma After Total Neoadjuvant Therapy to Improve Organ Preservation Rates
- NCT04263285 · started 2026-10 · NA
Treatment of Depression Post-SCI