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NCT04148001 · ClinicalTrials.gov registry record

Identifying and Genotyping Homozygous Familial Hypercholesterolemia (HoFH) Patients

A clinical trial of Homozygous Familial Hypercholesterolemia (HoFH), sponsored by REGENXBIO.

Completed
Registry status
4
Enrollment target
1
Study location

NCT04148001: Completed study of Homozygous Familial Hypercholesterolemia (HoFH), sponsored by REGENXBIO.

NCT04148001 is a study of Homozygous Familial Hypercholesterolemia (HoFH) that has completed, run by REGENXBIO. The registered enrollment target is 4 participants. The trial reports 1 study location across 1 state. According to ClinicalTrials.gov, the official US trial registry.

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The verdict

NCT04148001, a study of Homozygous Familial Hypercholesterolemia (HoFH), has completed, sponsored by REGENXBIO.

COMPLETED
Registry status
4 participants
Enrollment target
1
Study location

Study Summary

This study is designed to help identify patients with HoFH due to mutations in the LDLR as confirmed by genotyping.

Primary Outcome

The number of participants who have HoFH due to mutations in the LDLR (low density lipoprotein receptor) gene as confirmed by genetic testing.

Study Locations (1)

Florida

  • Excel Medical Clinical Trials, LLC - Boca Raton

Trial Details

FieldValue
Enrollment Target 4 participants
Start Date 2019-12-04
Est. Completion 2020-04-08
REGENXBIO

9 total trials

What the finished NCT04148001 record still lists

NCT04148001 is an observational study that tracks outcomes without assigning an intervention. The registry caps enrollment at 4 participants, a relatively small participant target.

The record links to 1 condition, with Homozygous Familial Hypercholesterolemia (HoFH) appearing as the primary indexed condition, and to 0 interventions.

NCT04148001 reports a single indexed study location in Florida.

Frequently Asked Questions

What is clinical trial NCT04148001 about?

NCT04148001 is a clinical study titled "Identifying and Genotyping Homozygous Familial Hypercholesterolemia (HoFH) Patients". This study is designed to help identify patients with HoFH due to mutations in the LDLR as confirmed by genotyping.

What is the current status of trial NCT04148001?

This trial is currently completed. The enrollment target is 4 participants. The study started on 2019-12-04. Estimated completion is 2020-04-08.

What conditions does trial NCT04148001 study?

This clinical trial studies the following conditions: Homozygous Familial Hypercholesterolemia (HoFH).

Who is sponsoring clinical trial NCT04148001?

This trial is sponsored by REGENXBIO, which has 9 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT04148001 being conducted?

This trial has 1 study location across Florida. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

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Source: ClinicalTrials.gov NCT04148001, the US trial registry maintained by the National Library of Medicine. NCT04148001 (small enrollment · single site footprint · completed) retrieved and formatted by PlainTrial, see methodology.