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NCT04098211 · ClinicalTrials.gov registry record
Longitudinal Assessment of Atypical Tripeptidyl Peptidase 1 Enzyme Deficiency Patients
A clinical trial, sponsored by Children's Hospital of Orange County.
- Active
- Registry status
- 5
- Enrollment target
NCT04098211: Active study, sponsored by Children's Hospital of Orange County.
NCT04098211 is a clinical trial that is active but no longer recruiting, run by Children's Hospital of Orange County. The registered enrollment target is 5 participants. According to ClinicalTrials.gov, the official US trial registry.
The verdict
NCT04098211 is active but no longer recruiting, sponsored by Children's Hospital of Orange County.
- ACTIVE NOT RECRUITING
- Registry status
- 5 participants
- Enrollment target
Study Summary
The purpose of this study is to gather information on the possible symptoms that patients with atypical neuronal ceroid lipofuscinosis type 2 (also known as aTPP1 or atypical tripeptidyl peptidase deficiency) have and how they change over time.
Primary Outcome
Modified Hamburg Rating Scale. The rating scale consists of two domains (motor function, language). Within each domain, a score from 0 to 3 is assigned and overall scores are calculated by summing the domain scores for final rating of 0 (severely impaired) to 6 (normal).
Trial Details
| Field | Value |
|---|---|
| Enrollment Target | 5 participants |
| Start Date | 2019-11-01 |
| Est. Completion | 2026-12 |
What the registry record for NCT04098211 still lists
NCT04098211 is an observational study that tracks outcomes without assigning an intervention. The registry caps enrollment at 5 participants, a relatively small participant target.
The record links to 0 conditions, and to 0 interventions.
NCT04098211 does not publish any study locations in the registry export this page uses.
Frequently Asked Questions
What is clinical trial NCT04098211 about?
NCT04098211 is a clinical study titled "Longitudinal Assessment of Atypical Tripeptidyl Peptidase 1 Enzyme Deficiency Patients". The purpose of this study is to gather information on the possible symptoms that patients with atypical neuronal ceroid lipofuscinosis type 2 (also known as aTPP1 or atypical tripeptidyl peptidase deficiency) have and how they change over time.
What is the current status of trial NCT04098211?
This trial is currently active not recruiting. The enrollment target is 5 participants. The study started on 2019-11-01. Estimated completion is 2026-12.
Who is sponsoring clinical trial NCT04098211?
This trial is sponsored by Children's Hospital of Orange County, which has 13 total clinical trials registered on ClinicalTrials.gov.
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