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NCT04049760 · ClinicalTrials.gov registry record · Phase 3
Safety, Pharmacodynamics, and Efficacy of Migalastat in Pediatric Subjects (Aged >12 Years) With Fabry Disease
A Phase 3 study, sponsored by Amicus Therapeutics.
- Completed
- Registry status
- Phase 3
- Development phase
- 16
- Enrollment target
NCT04049760 is a Phase 3 study that has completed, run by Amicus Therapeutics. The registered enrollment target is 16 participants.
The verdict
NCT04049760, a Phase 3 study, has completed, sponsored by Amicus Therapeutics.
- COMPLETED
- Registry status
- Phase 3
- Development phase
- 16 participants
- Enrollment target
Study Summary
This is a long-term, Open-label Study to Evaluate the Safety, Pharmacodynamics, and Efficacy of Migalastat in Subjects \> 12 Years of Age With Fabry Disease and Amenable GLA Variants
Interventions
- DRUG migalastat HCl 150 mg
Trial Details
| Field | Value |
|---|---|
| Enrollment Target | 16 participants |
| Start Date | 2019-10-11 |
| Est. Completion | 2024-11-29 |
| Phase | Phase 3 |
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Full Details on ClinicalTrials.gov ↗What the Registry Record Tells You About NCT04049760
The ClinicalTrials.gov registry entry for NCT04049760 describes a study currently listed as completed, categorized as Phase 3. The registered enrollment target is 16 participants, a figure that helps gauge the scale of data the investigators plan to collect. The listed sponsor is Amicus Therapeutics, which has 34 total studies on file at ClinicalTrials.gov.
The record links to 0 conditions, and to 1 intervention - of which migalastat HCl 150 mg is the first listed.
NCT04049760 reports 0 study locations.
Frequently Asked Questions
What is clinical trial NCT04049760 about?
NCT04049760 is a clinical study titled "Safety, Pharmacodynamics, and Efficacy of Migalastat in Pediatric Subjects (Aged >12 Years) With Fabry Disease". This is a long-term, Open-label Study to Evaluate the Safety, Pharmacodynamics, and Efficacy of Migalastat in Subjects \> 12 Years of Age With Fabry Disease and Amenable GLA Variants
What is the current status of trial NCT04049760?
This trial is currently completed. It is a Phase 3 study. The enrollment target is 16 participants. The study started on 2019-10-11. Estimated completion is 2024-11-29.
What interventions are being tested in trial NCT04049760?
The interventions under investigation include: migalastat HCl 150 mg (DRUG).
Who is sponsoring clinical trial NCT04049760?
This trial is sponsored by Amicus Therapeutics, which has 34 total clinical trials registered on ClinicalTrials.gov.
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