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NCT04004065 · ClinicalTrials.gov registry record · Phase 2

Two-Part Study for Dose Determination of Vesleteplirsen (SRP-5051) (Part A), Then Dose Expansion (Part B) in Participants With Duchenne Muscular Dystrophy Amenable to Exon 51-Skipping Treatment

A Phase 2 study, sponsored by Sarepta Therapeutics.

Terminated
Registry status
Phase 2
Development phase
62
Enrollment target

NCT04004065 is a Phase 2 study that was terminated before completion, run by Sarepta Therapeutics. The registered enrollment target is 62 participants.

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The verdict

NCT04004065, a Phase 2 study, was terminated before completion, sponsored by Sarepta Therapeutics.

TERMINATED
Registry status
Phase 2
Development phase
62 participants
Enrollment target

Study Summary

This study will be comprised of 2 parts: 1) Part A (Multiple Ascending Dose \[MAD\]) will be conducted to evaluate the safety and tolerability of vesleteplirsen at MAD levels to determine the maximum tolerated dose (MTD), and 2) Part B will be conducted to further evaluate the vesleteplirsen doses selected in Part A. Participants enrolling in Part B will be those who completed Part A or Study 5051-102 (NCT03675126) and meet applicable eligibility criteria for Part B, as well as additional participants who meet applicable eligibility criteria for enrollment at the beginning of Part B.

Interventions

  • DRUG Vesleteplirsen

Trial Details

FieldValue
Enrollment Target 62 participants
Start Date 2019-06-26
Est. Completion 2025-02-07
Phase Phase 2

Sponsor

Sarepta Therapeutics

33 total trials

What the Registry Record Tells You About NCT04004065

The ClinicalTrials.gov registry entry for NCT04004065 describes a study currently listed as terminated, categorized as Phase 2. The registered enrollment target is 62 participants, a figure that helps gauge the scale of data the investigators plan to collect. The listed sponsor is Sarepta Therapeutics, which has 33 total studies on file at ClinicalTrials.gov.

The record links to 0 conditions, and to 1 intervention - of which Vesleteplirsen is the first listed.

NCT04004065 reports 0 study locations.

Frequently Asked Questions

What is clinical trial NCT04004065 about?

NCT04004065 is a clinical study titled "Two-Part Study for Dose Determination of Vesleteplirsen (SRP-5051) (Part A), Then Dose Expansion (Part B) in Participants With Duchenne Muscular Dystrophy Amenable to Exon 51-Skipping Treatment". This study will be comprised of 2 parts: 1) Part A (Multiple Ascending Dose \[MAD\]) will be conducted to evaluate the safety and tolerability of vesleteplirsen at MAD levels to determine the maximum tolerated dose (MTD), and 2) Part B will be conducted to further evaluate the vesleteplirsen doses s...

What is the current status of trial NCT04004065?

This trial is currently terminated. It is a Phase 2 study. The enrollment target is 62 participants. The study started on 2019-06-26. Estimated completion is 2025-02-07.

What interventions are being tested in trial NCT04004065?

The interventions under investigation include: Vesleteplirsen (DRUG).

Who is sponsoring clinical trial NCT04004065?

This trial is sponsored by Sarepta Therapeutics, which has 33 total clinical trials registered on ClinicalTrials.gov.

Data sourced from official public datasets. See our methodology for details. Retrieved and formatted by PlainTrial Editorial

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This page mirrors this trial's own ClinicalTrials.gov registry record, live from the dataset. See our editorial standards & corrections policy, the methodology behind these numbers, or report a data error.