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NCT04002531 · ClinicalTrials.gov registry record · NA
A One Visit Follow Up of Adults With Fabry Disease Who Started Long-term Enzyme Replacement Therapy As Children
A NA study, sponsored by Baylor Research Institute.
- Completed
- Registry status
- NA
- Development phase
- 5
- Enrollment target
NCT04002531: Completed NA study, sponsored by Baylor Research Institute.
NCT04002531 is a NA study that has completed, run by Baylor Research Institute. The registered enrollment target is 5 participants, below the 1,404-participant average among 58,714 other NA trials with a reported enrollment target (100% lower). According to ClinicalTrials.gov, the official US trial registry.
The verdict
NCT04002531, a NA study, has completed, sponsored by Baylor Research Institute.
- COMPLETED
- Registry status
- NA
- Development phase
- 5 participants
- Enrollment target
Study Summary
The objective of this study is to obtain follow up data on a cohort of well-studied patients with Fabry disease who have been on ERT since childhood for a total of about 15 years.
Primary Outcome
Change in eGFR since previous participation in study "Replagal Enzyme Replacement Therapy for Children With Fabry Disease" - NCT00084084
Interventions
- PROCEDURE Echocardiogram
- PROCEDURE Blood draw
- OTHER General and Neurological examination
- OTHER Vital signs
- PROCEDURE 12 lead electrocardiogram
Trial Details
| Field | Value |
|---|---|
| Enrollment Target | 5 participants |
| Start Date | 2018-11-10 |
| Est. Completion | 2019-12-13 |
| Phase | NA |
What the finished NCT04002531 record still lists
NCT04002531 is an interventional study that assigns participants to a tested intervention. The registry caps enrollment at 5 participants, a relatively small participant target, below the 1,404-participant average among 58,714 other NA trials with a reported enrollment target (100% lower).
The record links to 0 conditions, and to 5 interventions - of which Echocardiogram is the first listed.
NCT04002531 does not publish any study locations in the registry export this page uses.
Frequently Asked Questions
What is clinical trial NCT04002531 about?
NCT04002531 is a clinical study titled "A One Visit Follow Up of Adults With Fabry Disease Who Started Long-term Enzyme Replacement Therapy As Children". The objective of this study is to obtain follow up data on a cohort of well-studied patients with Fabry disease who have been on ERT since childhood for a total of about 15 years.
What is the current status of trial NCT04002531?
This trial is currently completed. It is a NA study. The enrollment target is 5 participants. The study started on 2018-11-10. Estimated completion is 2019-12-13.
What interventions are being tested in trial NCT04002531?
The interventions under investigation include: Echocardiogram (PROCEDURE), Blood draw (PROCEDURE), General and Neurological examination (OTHER), Vital signs (OTHER), 12 lead electrocardiogram (PROCEDURE).
Who is sponsoring clinical trial NCT04002531?
This trial is sponsored by Baylor Research Institute, which has 180 total clinical trials registered on ClinicalTrials.gov.
Learn More About Clinical Trials
How this trial's enrollment target compares
Where NCT04002531's enrollment target sits among peer trials
5 1988th of 2000 higher than 5 of 2,000 other NA trials
participants (enrollment target), bucketed by value
Each bar is a band; taller bars hold more other NA trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.
Source ClinicalTrials.gov registry export · 2026-08-08
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