Medical Information Only. Always consult your healthcare provider before enrolling in any clinical trial.

NCT03597399 · ClinicalTrials.gov registry record

A Patient Registry Study for Patients Treated With Voretigene Neparvovec in US

A clinical trial, sponsored by Spark Therapeutics.

Completed
Registry status
87
Enrollment target

NCT03597399: Completed study, sponsored by Spark Therapeutics.

NCT03597399 is a clinical trial that has completed, run by Spark Therapeutics. The registered enrollment target is 87 participants. According to ClinicalTrials.gov, the official US trial registry.

View on ClinicalTrials.gov ↗

View your shortlist →

The verdict

NCT03597399 has completed, sponsored by Spark Therapeutics.

COMPLETED
Registry status
87 participants
Enrollment target

Study Summary

The objective of this study is to collect long-term safety information (i.e., for 5 years after treatment) associated with voretigene neparvovec-rzyl (vector and/or transgene), its subretinal injection procedure, the concomitant use of corticosteroids, or a combination of these procedures and products. The enrollment period will last for two years from the first treatment following product approval (through 31March2020) and include a minimum of 40 patients.

Primary Outcome

adverse events

Interventions

  • BIOLOGICAL AAV2-hRPE65v2,voretigene neparvovec-rzyl

Trial Details

FieldValue
Enrollment Target 87 participants
Start Date 2019-01-10
Est. Completion 2025-06-30
Spark Therapeutics

13 total trials

What the finished NCT03597399 record still lists

NCT03597399 is an observational study that tracks outcomes without assigning an intervention. The registry caps enrollment at 87 participants, a relatively small participant target.

The record links to 0 conditions, and to 1 intervention - of which AAV2-hRPE65v2,voretigene neparvovec-rzyl is the first listed.

NCT03597399 does not publish any study locations in the registry export this page uses.

Frequently Asked Questions

What is clinical trial NCT03597399 about?

NCT03597399 is a clinical study titled "A Patient Registry Study for Patients Treated With Voretigene Neparvovec in US". The objective of this study is to collect long-term safety information (i.e., for 5 years after treatment) associated with voretigene neparvovec-rzyl (vector and/or transgene), its subretinal injection procedure, the concomitant use of corticosteroids, or a combination of these procedures and produc...

What is the current status of trial NCT03597399?

This trial is currently completed. The enrollment target is 87 participants. The study started on 2019-01-10. Estimated completion is 2025-06-30.

What interventions are being tested in trial NCT03597399?

The interventions under investigation include: AAV2-hRPE65v2,voretigene neparvovec-rzyl (BIOLOGICAL).

Who is sponsoring clinical trial NCT03597399?

This trial is sponsored by Spark Therapeutics, which has 13 total clinical trials registered on ClinicalTrials.gov.

Nationwide trials with similar profiles

Cross-condition peers matched on enrollment target and registry start date, not the same-condition list above.

Similar enrollment target

  • NCT03292601 · 87 participants · NA

    Brace Monitoring for Adolescent Idiopathic Scoliosis (AIS)

  • NCT04291105 · 87 participants · Phase 2

    Phase 2 Trial of Voyager V1 in Combination With Cemiplimab in Cancer Patients

  • NCT04565795 · 87 participants · NA

    Safety and Device Performance of the Uriprene® Degradable Temporary Ureteral Stent Following Uncomplicated Ureteroscopy

  • NCT05607004 · 87 participants · Phase 2

    (Z)-Endoxifen for the Treatment of Premenopausal Women With ER+/HER2- Breast Cancer

Similar registry start date

  • NCT05962346 · started 2026-12 · NA

    Fetal Endoscopic Tracheal Occlusion for Congenital Diaphragmatic Hernia

  • NCT07125183 · started 2026-12 · Phase 2

    Study on Efficacy and Tolerability of Weekly Doxorubicin in Elderly Patients With Advanced or Metastatic Leiomyosarcoma

  • NCT07292298 · started 2026-11 · Phase 2

    Phase 2 Single-Arm Rectal Cancer Brachytherapy for Patients With Low-Lying Residual Adenocarcinoma After Total Neoadjuvant Therapy to Improve Organ Preservation Rates

  • NCT04263285 · started 2026-10 · NA

    Treatment of Depression Post-SCI

Source: ClinicalTrials.gov NCT03597399, the US trial registry maintained by the National Library of Medicine. NCT03597399 (small enrollment · none site footprint · completed) retrieved and formatted by PlainTrial, see methodology.