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NCT03597399 · ClinicalTrials.gov registry record

A Patient Registry Study for Patients Treated With Voretigene Neparvovec in US

A clinical trial, sponsored by Spark Therapeutics.

Completed
Registry status
87
Enrollment target

NCT03597399 is a clinical trial that has completed, run by Spark Therapeutics. The registered enrollment target is 87 participants.

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The verdict

NCT03597399 has completed, sponsored by Spark Therapeutics.

COMPLETED
Registry status
87 participants
Enrollment target

Study Summary

The objective of this study is to collect long-term safety information (i.e., for 5 years after treatment) associated with voretigene neparvovec-rzyl (vector and/or transgene), its subretinal injection procedure, the concomitant use of corticosteroids, or a combination of these procedures and products. The enrollment period will last for two years from the first treatment following product approval (through 31March2020) and include a minimum of 40 patients.

Interventions

  • BIOLOGICAL AAV2-hRPE65v2,voretigene neparvovec-rzyl

Trial Details

FieldValue
Enrollment Target 87 participants
Start Date 2019-01-10
Est. Completion 2025-06-30

Sponsor

Spark Therapeutics

13 total trials

What the Registry Record Tells You About NCT03597399

The ClinicalTrials.gov registry entry for NCT03597399 describes a study currently listed as completed, categorized as an unspecified phase. The registered enrollment target is 87 participants, a figure that helps gauge the scale of data the investigators plan to collect. The listed sponsor is Spark Therapeutics, which has 13 total studies on file at ClinicalTrials.gov.

The record links to 0 conditions, and to 1 intervention - of which AAV2-hRPE65v2,voretigene neparvovec-rzyl is the first listed.

NCT03597399 reports 0 study locations.

Frequently Asked Questions

What is clinical trial NCT03597399 about?

NCT03597399 is a clinical study titled "A Patient Registry Study for Patients Treated With Voretigene Neparvovec in US". The objective of this study is to collect long-term safety information (i.e., for 5 years after treatment) associated with voretigene neparvovec-rzyl (vector and/or transgene), its subretinal injection procedure, the concomitant use of corticosteroids, or a combination of these procedures and produc...

What is the current status of trial NCT03597399?

This trial is currently completed. The enrollment target is 87 participants. The study started on 2019-01-10. Estimated completion is 2025-06-30.

What interventions are being tested in trial NCT03597399?

The interventions under investigation include: AAV2-hRPE65v2,voretigene neparvovec-rzyl (BIOLOGICAL).

Who is sponsoring clinical trial NCT03597399?

This trial is sponsored by Spark Therapeutics, which has 13 total clinical trials registered on ClinicalTrials.gov.

Data sourced from official public datasets. See our methodology for details. Retrieved and formatted by PlainTrial Editorial

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This page mirrors this trial's own ClinicalTrials.gov registry record, live from the dataset. See our editorial standards & corrections policy, the methodology behind these numbers, or report a data error.