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NCT02993796 · ClinicalTrials.gov registry record
Krabbe Disease Global Patient Registry
A clinical trial of Krabbe Disease, sponsored by State University of New York at Buffalo.
- Recruiting
- Registry status
- 60
- Enrollment target
- 1
- Study location
NCT02993796: Recruiting study of Krabbe Disease, sponsored by State University of New York at Buffalo.
NCT02993796 is a study of Krabbe Disease that is actively recruiting participants, run by State University of New York at Buffalo. The registered enrollment target is 60 participants, below the 404-participant average among 4 other Krabbe Disease trials with a reported enrollment target (85% lower). The trial reports 1 study location across 1 state. According to ClinicalTrials.gov, the official US trial registry.
The verdict
NCT02993796, a study of Krabbe Disease, is actively recruiting participants, sponsored by State University of New York at Buffalo.
- RECRUITING
- Registry status
- 60 participants
- Enrollment target
- 1
- Study location
Study Summary
The purpose of this study is to develop a clinical database of individuals diagnosed with Krabbe disease in order to determine which symptoms herald the onset of clinical disease in the various phenotypes of Krabbe disease; to determine whether level of GALC enzyme activity, or a specific genetic mutation predict the clinical course; and to determine which neurodiagnostic tests predict onset and/or severity of the disease.
Primary Outcome
The longevity of participants will be recorded using their date of death, or conclusion of this study, whichever occurs first.
Conditions Studied
Study Locations (1)
New York
- State University of New York at Buffalo - Buffalo
Trial Details
| Field | Value |
|---|---|
| Enrollment Target | 60 participants |
| Start Date | 2014-09 |
| Est. Completion | 2026-09 |
What NCT02993796 shows while recruiting
NCT02993796 is an observational study that tracks outcomes without assigning an intervention. The registry caps enrollment at 60 participants, a relatively small participant target, below the 404-participant average among 4 other Krabbe Disease trials with a reported enrollment target (85% lower).
The record links to 1 condition, with Krabbe Disease appearing as the primary indexed condition, and to 0 interventions.
NCT02993796 reports a single indexed study location in New York.
Frequently Asked Questions
What is clinical trial NCT02993796 about?
NCT02993796 is a clinical study titled "Krabbe Disease Global Patient Registry". The purpose of this study is to develop a clinical database of individuals diagnosed with Krabbe disease in order to determine which symptoms herald the onset of clinical disease in the various phenotypes of Krabbe disease; to determine whether level of GALC enzyme activity, or a specific genetic mu...
What is the current status of trial NCT02993796?
This trial is currently recruiting. The enrollment target is 60 participants. The study started on 2014-09. Estimated completion is 2026-09.
What conditions does trial NCT02993796 study?
This clinical trial studies the following conditions: Krabbe Disease.
Who is sponsoring clinical trial NCT02993796?
This trial is sponsored by State University of New York at Buffalo, which has 243 total clinical trials registered on ClinicalTrials.gov.
Where is trial NCT02993796 being conducted?
This trial has 1 study location across New York. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.
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