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NCT02074839 · ClinicalTrials.gov registry record · Phase 1

Study of Orally Administered AG-120 in Subjects With Advanced Hematologic Malignancies With an IDH1 Mutation

A Phase 1 study of Myelodysplastic Syndromes and Untreated AML, sponsored by Institut de Recherches Internationales Servier.

Recruiting
Registry status
Phase 1
Development phase
291
Enrollment target
20
Study locations

NCT02074839: Recruiting Phase 1 study of Myelodysplastic Syndromes and Untreated AML, sponsored by Institut de Recherches Internationales Servier.

NCT02074839 is a Phase 1 study of Myelodysplastic Syndromes and Untreated AML that is actively recruiting participants, run by Institut de Recherches Internationales Servier. The registered enrollment target is 291 participants, roughly in line with the 283-participant average among 173 other Myelodysplastic Syndromes trials with a reported enrollment target. The trial reports 20 study locations across 14 states. According to ClinicalTrials.gov, the official US trial registry.

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The verdict

NCT02074839, a Phase 1 study of Myelodysplastic Syndromes and Untreated AML, is actively recruiting participants, sponsored by Institut de Recherches Internationales Servier.

RECRUITING
Registry status
Phase 1
Development phase
291 participants
Enrollment target
20
Study locations

Study Summary

The purpose of this Phase I, multicenter study is to evaluate the safety, pharmacokinetics, pharmacodynamics and clinical activity of AG-120 in advanced hematologic malignancies that harbor an IDH1 mutation. The first portion of the study is a dose escalation phase where cohorts of patients will receive ascending oral doses of AG-120 to determine maximum tolerated dose (MTD) and/or the recommended Phase II dose. The second portion of the study is a dose expansion phase where four cohorts of patients will receive AG-120 to further evaluate the safety, tolerability, and clinical activity of the recommended Phase II dose. Additionally, the study includes a substudy evaluating the safety and tolerability, clinical activity, pharmacokinetics, and pharmacodynamics of AG-120 in subjects with relapsed or refractory myelodysplastic syndrome with an IDH1 mutation. Anticipated time on study treatment is until disease progression or unacceptable toxicity occurs.

Interventions

  • DRUG AG-120

Study Locations (20)

California

  • City of Hope - Duarte
  • University of California-Los Angeles - Los Angeles
  • University of California-San Francisco - San Francisco

Florida

  • Mayo Clinic-Jacksonville - Jacksonville
  • University of Miami - Miami
  • Moffit Cancer Center - Tampa

Massachusetts

  • Massachusetts General Hospital - Boston
  • Dana Farber Cancer Institute - Boston

New York

  • Memorial Sloan Kettering Cancer Center - New York
  • Cornell Cancer Center - New York

Alabama

  • University of Alabama at Birmingham - Birmingham

Arizona

  • Mayo Clinic-AZ - Phoenix

Colorado

  • University of Colorado Denver - Aurora

Georgia

  • Emory University - Atlanta

Trial Details

FieldValue
Enrollment Target 291 participants
Start Date 2014-03-01
Est. Completion 2026-03
Phase Phase 1

What NCT02074839 shows while recruiting

NCT02074839 is an interventional study that assigns participants to a tested intervention. The registered 291 participants enrollment target is mid-sized for trials with a published cap, roughly in line with the 283-participant average among 173 other Myelodysplastic Syndromes trials with a reported enrollment target.

The record links to 4 conditions, with Myelodysplastic Syndromes appearing as the primary indexed condition, and to 1 intervention - of which AG-120 is the first listed.

NCT02074839 names 20 study sites across 14 states, led by California, Florida, Massachusetts.

Frequently Asked Questions

What is clinical trial NCT02074839 about?

NCT02074839 is a clinical study titled "Study of Orally Administered AG-120 in Subjects With Advanced Hematologic Malignancies With an IDH1 Mutation". The purpose of this Phase I, multicenter study is to evaluate the safety, pharmacokinetics, pharmacodynamics and clinical activity of AG-120 in advanced hematologic malignancies that harbor an IDH1 mutation. The first portion of the study is a dose escalation phase where cohorts of patients will rec...

What is the current status of trial NCT02074839?

This trial is currently recruiting. It is a Phase 1 study. The enrollment target is 291 participants. The study started on 2014-03-01. Estimated completion is 2026-03.

What conditions does trial NCT02074839 study?

This clinical trial studies the following conditions: Myelodysplastic Syndromes, Untreated AML, Relapsed or Refractory Acute Myeloid Leukemia (AML), Other IDH1-mutated Positive Hematologic Malignancies.

What interventions are being tested in trial NCT02074839?

The interventions under investigation include: AG-120 (DRUG).

Who is sponsoring clinical trial NCT02074839?

This trial is sponsored by Institut de Recherches Internationales Servier, which has 27 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT02074839 being conducted?

This trial has 20 study locations across Alabama, Arizona, California, Colorado, Florida. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

Similar trials for Myelodysplastic Syndromes

Matched on the same primary condition, ranked to surface studies in the same phase first, then by recruiting status, no relevance scoring or editorial curation.

Where NCT02074839's enrollment target sits among peer trials

291 23rd of 173 higher than 151 of 173 other Myelodysplastic Syndromes trials

participants (enrollment target), bucketed by value

Each bar is a band; taller bars hold more other Myelodysplastic Syndromes trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.

Source ClinicalTrials.gov registry export · 2026-08-08

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Source: ClinicalTrials.gov NCT02074839, the US trial registry maintained by the National Library of Medicine. NCT02074839 (mid enrollment · wide site footprint · recruiting) retrieved and formatted by PlainTrial, see methodology.