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NCT01938014 · ClinicalTrials.gov registry record
Lysosomal Storage Disease: Health, Development, and Functional Outcome Surveillance in Preschool Children
A clinical trial, sponsored by University of Chicago.
- Completed
- Registry status
- 19
- Enrollment target
NCT01938014: Completed study, sponsored by University of Chicago.
NCT01938014 is a clinical trial that has completed, run by University of Chicago. The registered enrollment target is 19 participants. According to ClinicalTrials.gov, the official US trial registry.
The verdict
NCT01938014 has completed, sponsored by University of Chicago.
- COMPLETED
- Registry status
- 19 participants
- Enrollment target
Study Summary
Hypothesis: Children diagnosed with a lysosomal disease will exhibit developmental, adaptive, and behavioral strengths and difficulties depending upon 1) biomedical risk factors (i.e. the specific genetic disorder responsible for the illness); 2) available modifying interventions, whether medical or behavioral; and 3) social risks in the children's families, neighborhoods and communities. A valid and reliable telephone-based surveillance system can successfully collect the data required to elucidate these developmental, adaptive and behavioral strengths and difficulties.
Primary Outcome
Using the technique of telephone-based interviews with the child's care-giver(s), the investigators will obtain and record verbal responses to a variety of standardized assessment tools which seek to ascertain the lysosomal disease-affected child's health status.
Trial Details
| Field | Value |
|---|---|
| Enrollment Target | 19 participants |
| Start Date | 2009-01 |
| Est. Completion | 2016-07-23 |
What the finished NCT01938014 record still lists
NCT01938014 is an observational study that tracks outcomes without assigning an intervention. The registry caps enrollment at 19 participants, a relatively small participant target.
The record links to 0 conditions, and to 0 interventions.
NCT01938014 does not publish any study locations in the registry export this page uses.
Frequently Asked Questions
What is clinical trial NCT01938014 about?
NCT01938014 is a clinical study titled "Lysosomal Storage Disease: Health, Development, and Functional Outcome Surveillance in Preschool Children". Hypothesis: Children diagnosed with a lysosomal disease will exhibit developmental, adaptive, and behavioral strengths and difficulties depending upon 1) biomedical risk factors (i.e. the specific genetic disorder responsible for the illness); 2) available modifying interventions, whether medical or...
What is the current status of trial NCT01938014?
This trial is currently completed. The enrollment target is 19 participants. The study started on 2009-01. Estimated completion is 2016-07-23.
Who is sponsoring clinical trial NCT01938014?
This trial is sponsored by University of Chicago, which has 796 total clinical trials registered on ClinicalTrials.gov.
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