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NCT01601535 · ClinicalTrials.gov registry record · Phase 1

Study of MLN8237 in Combination With Irinotecan and Temozolomide

A Phase 1 study of Neuroblastoma, sponsored by New Approaches to Neuroblastoma Therapy Consortium.

Completed
Registry status
Phase 1
Development phase
54
Enrollment target
13
Study locations

NCT01601535: Completed Phase 1 study of Neuroblastoma, sponsored by New Approaches to Neuroblastoma Therapy Consortium.

NCT01601535 is a Phase 1 study of Neuroblastoma that has completed, run by New Approaches to Neuroblastoma Therapy Consortium. The registered enrollment target is 54 participants, below the 238-participant average among 94 other Neuroblastoma trials with a reported enrollment target (77% lower). The trial reports 13 study locations across 11 states. According to ClinicalTrials.gov, the official US trial registry.

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The verdict

NCT01601535, a Phase 1 study of Neuroblastoma, has completed, sponsored by New Approaches to Neuroblastoma Therapy Consortium.

COMPLETED
Registry status
Phase 1
Development phase
54 participants
Enrollment target
13
Study locations

Study Summary

The goal of the first part of this clinical trial (Phase I portion) is to study the side effects, drug breakdown (pharmacokinetics), and dosing of the drug MLN8237 when added to standard chemotherapy drugs, irinotecan and temozolomide. The goal of the second part of this clinical trial (Phase II portion) is to learn how many children and young adults show improvements in their neuroblastoma when treated with the combination of MLN8237, irinotecan, and temozolomide.

Primary Outcome

The MTD was the highest dose level tested at which fewer than two of six patients had first course DLT. Hematologic DLT was defined as grade 4 neutropenia for more than 7 days, need for platelet transfusion for a platelet count of less than 20,000/mL twice within a 7-day period, or greater than 14-day delay in the start of a subsequent course because of neutropenia or thrombocytopenia. Nonhematologic DLT was defined as any nonhematologic toxicity that delayed the start of a subsequent cycle by m

Conditions Studied

Interventions

  • DRUG Temozolomide
  • DRUG Irinotecan
  • DRUG MLN8237

Study Locations (13)

California

  • Children's Hospital Los Angeles - Los Angeles
  • Lucile Packard Children's Hospital at Stanford University Medical Center - Palo Alto
  • UCSF Helen Diller Family Comprehensive Cancer Center - San Francisco

Colorado

  • Children Hospital of Colorado - Aurora

Georgia

  • Children's Healthcare of Atlanta - Atlanta

Illinois

  • University of Chicago Comer Children's Hospital - Chicago

Massachusetts

  • Childrens Hospital Boston, Dana-Farber Cancer Institute. - Boston

Michigan

  • University of Michigan Comprehensive Cancer Center - Ann Arbor

Ohio

  • Cincinnati Children's Hospital Medical Center - Cincinnati

Pennsylvania

  • Children's Hospital of Philadelphia - Philadelphia

Trial Details

FieldValue
Enrollment Target 54 participants
Start Date 2012-05
Est. Completion 2018-07-25
Phase Phase 1

What the finished NCT01601535 record still lists

NCT01601535 is an interventional study that assigns participants to a tested intervention. The registry caps enrollment at 54 participants, a relatively small participant target, below the 238-participant average among 94 other Neuroblastoma trials with a reported enrollment target (77% lower).

The record links to 1 condition, with Neuroblastoma appearing as the primary indexed condition, and to 3 interventions - of which Temozolomide is the first listed.

NCT01601535 lists 13 locations in 11 states (California, Colorado, Georgia).

Frequently Asked Questions

What is clinical trial NCT01601535 about?

NCT01601535 is a clinical study titled "Study of MLN8237 in Combination With Irinotecan and Temozolomide". The goal of the first part of this clinical trial (Phase I portion) is to study the side effects, drug breakdown (pharmacokinetics), and dosing of the drug MLN8237 when added to standard chemotherapy drugs, irinotecan and temozolomide. The goal of the second part of this clinical trial (Phase II po...

What is the current status of trial NCT01601535?

This trial is currently completed. It is a Phase 1 study. The enrollment target is 54 participants. The study started on 2012-05. Estimated completion is 2018-07-25.

What conditions does trial NCT01601535 study?

This clinical trial studies the following conditions: Neuroblastoma.

What interventions are being tested in trial NCT01601535?

The interventions under investigation include: Temozolomide (DRUG), Irinotecan (DRUG), MLN8237 (DRUG).

Who is sponsoring clinical trial NCT01601535?

This trial is sponsored by New Approaches to Neuroblastoma Therapy Consortium, which has 23 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT01601535 being conducted?

This trial has 13 study locations across California, Colorado, Georgia, Illinois, Massachusetts. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

Similar trials for Neuroblastoma

Matched on the same primary condition, ranked to surface studies in the same phase first, then by recruiting status, no relevance scoring or editorial curation.

Where NCT01601535's enrollment target sits among peer trials

54 45th of 94 higher than 50 of 94 other Neuroblastoma trials

participants (enrollment target), bucketed by value

Each bar is a band; taller bars hold more other Neuroblastoma trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.

Source ClinicalTrials.gov registry export · 2026-08-08

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Source: ClinicalTrials.gov NCT01601535, the US trial registry maintained by the National Library of Medicine. NCT01601535 (small enrollment · multi site footprint · completed) retrieved and formatted by PlainTrial, see methodology.