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NCT01560286 · ClinicalTrials.gov registry record · Phase 2

A Study to Evaluate Subcutaneously Administered rAvPAL-PEG in Patients With Phenylketonuria for 24 Weeks

A Phase 2 study of Phenylketonuria, sponsored by BioMarin Pharmaceutical.

Completed
Registry status
Phase 2
Development phase
24
Enrollment target
6
Study locations

NCT01560286 is a Phase 2 study of Phenylketonuria that has completed, run by BioMarin Pharmaceutical. The registered enrollment target is 24 participants, below the 97-participant average among 12 other Phenylketonuria trials with a reported enrollment target (75% lower). The trial reports 6 study locations across 6 states.

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The verdict

NCT01560286, a Phase 2 study of Phenylketonuria, has completed, sponsored by BioMarin Pharmaceutical.

COMPLETED
Registry status
Phase 2
Development phase
24 participants
Enrollment target
6
Study locations

Study Summary

The primary objective of the study is to evaluate the effect of dosing regimens of multiple subcutaneous (SC) doses of rAvPAL-PEG to induce an early and sustained Phe reduction while decreasing the frequency and severity of hypersensitivity reactions in patients with PKU.

Conditions Studied

Interventions

  • BIOLOGICAL BMN 165 (rAvPAL-PEG)

Study Locations (6)

Colorado

  • The Children's Hospital - Aurora

Florida

  • University of Florida, Gainesville - Gainesville

Massachusetts

  • Children's Hospital Boston - Boston

Nebraska

  • Nebraska Medical Center - Omaha

New York

  • Albany Medical Center - Albany

Utah

  • University of Utah Hospital - Salt Lake City

Trial Details

FieldValue
Enrollment Target 24 participants
Start Date 2012-05
Est. Completion 2015-07
Phase Phase 2

Sponsor

BioMarin Pharmaceutical

80 total trials

What the Registry Record Tells You About NCT01560286

The ClinicalTrials.gov registry entry for NCT01560286 describes a study currently listed as completed, categorized as Phase 2. The registered enrollment target is 24 participants, a figure that helps gauge the scale of data the investigators plan to collect, below the 97-participant average among 12 other Phenylketonuria trials with a reported enrollment target (75% lower). The listed sponsor is BioMarin Pharmaceutical, which has 80 total studies on file at ClinicalTrials.gov.

The record links to 1 condition, with Phenylketonuria appearing as the primary indexed condition, and to 1 intervention - of which BMN 165 (rAvPAL-PEG) is the first listed.

NCT01560286 reports 6 study locations spanning 6 distinct geographic areas - top geographies include Colorado, Florida, Massachusetts.

Frequently Asked Questions

What is clinical trial NCT01560286 about?

NCT01560286 is a clinical study titled "A Study to Evaluate Subcutaneously Administered rAvPAL-PEG in Patients With Phenylketonuria for 24 Weeks". The primary objective of the study is to evaluate the effect of dosing regimens of multiple subcutaneous (SC) doses of rAvPAL-PEG to induce an early and sustained Phe reduction while decreasing the frequency and severity of hypersensitivity reactions in patients with PKU.

What is the current status of trial NCT01560286?

This trial is currently completed. It is a Phase 2 study. The enrollment target is 24 participants. The study started on 2012-05. Estimated completion is 2015-07.

What conditions does trial NCT01560286 study?

This clinical trial studies the following conditions: Phenylketonuria.

What interventions are being tested in trial NCT01560286?

The interventions under investigation include: BMN 165 (rAvPAL-PEG) (BIOLOGICAL).

Who is sponsoring clinical trial NCT01560286?

This trial is sponsored by BioMarin Pharmaceutical, which has 80 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT01560286 being conducted?

This trial has 6 study locations across Colorado, Florida, Massachusetts, Nebraska, New York. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

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Data sourced from official public datasets. See our methodology for details. Retrieved and formatted by PlainTrial Editorial

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This page mirrors this trial's own ClinicalTrials.gov registry record, live from the dataset. See our editorial standards & corrections policy, the methodology behind these numbers, or report a data error.