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NCT00272857 · ClinicalTrials.gov registry record · Phase 1
Bone Marrow Cell Gene Transfer in Individuals With Fanconi Anemia
A Phase 1 study, sponsored by Boston Children's Hospital.
- Completed
- Registry status
- Phase 1
- Development phase
- 3
- Enrollment target
NCT00272857: Completed Phase 1 study, sponsored by Boston Children's Hospital.
NCT00272857 is a Phase 1 study that has completed, run by Boston Children's Hospital. The registered enrollment target is 3 participants, below the 60-participant average among 29,502 other Phase 1 trials with a reported enrollment target (95% lower). According to ClinicalTrials.gov, the official US trial registry.
The verdict
NCT00272857, a Phase 1 study, has completed, sponsored by Boston Children's Hospital.
- COMPLETED
- Registry status
- Phase 1
- Development phase
- 3 participants
- Enrollment target
Study Summary
Fanconi anemia (FA) is a disease that affects an individual's bone marrow. It is caused by a defective gene in the bone marrow cells that produce various types of blood cells. Individuals with FA may experience fatigue, bleeding, and increased infections. The purpose of this study is to evaluate the safety and effectiveness of a gene transfer procedure in generating new, healthy cells in individuals with FA.
Interventions
- GENETIC Retrovirus Construct
Trial Details
| Field | Value |
|---|---|
| Enrollment Target | 3 participants |
| Start Date | 2004-08 |
| Est. Completion | 2007-10 |
| Phase | Phase 1 |
What the finished NCT00272857 record still lists
NCT00272857 is an interventional study that assigns participants to a tested intervention. The registry caps enrollment at 3 participants, a relatively small participant target, below the 60-participant average among 29,502 other Phase 1 trials with a reported enrollment target (95% lower).
The record links to 0 conditions, and to 1 intervention - of which Retrovirus Construct is the first listed.
NCT00272857 does not publish any study locations in the registry export this page uses.
Frequently Asked Questions
What is clinical trial NCT00272857 about?
NCT00272857 is a clinical study titled "Bone Marrow Cell Gene Transfer in Individuals With Fanconi Anemia". Fanconi anemia (FA) is a disease that affects an individual's bone marrow. It is caused by a defective gene in the bone marrow cells that produce various types of blood cells. Individuals with FA may experience fatigue, bleeding, and increased infections. The purpose of this study is to evaluate the...
What is the current status of trial NCT00272857?
This trial is currently completed. It is a Phase 1 study. The enrollment target is 3 participants. The study started on 2004-08. Estimated completion is 2007-10.
What interventions are being tested in trial NCT00272857?
The interventions under investigation include: Retrovirus Construct (GENETIC).
Who is sponsoring clinical trial NCT00272857?
This trial is sponsored by Boston Children's Hospital, which has 462 total clinical trials registered on ClinicalTrials.gov.
Learn More About Clinical Trials
How this trial's enrollment target compares
Where NCT00272857's enrollment target sits among peer trials
3 1999th of 2000 higher than 1 of 2,000 other Phase 1 trials
participants (enrollment target), bucketed by value
Each bar is a band; taller bars hold more other Phase 1 trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.
Source ClinicalTrials.gov registry export · 2026-08-08
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