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NCT00272844 · ClinicalTrials.gov registry record · Phase 1

Treatment of the Cholesterol Defect in Smith-Lemli-Opitz Syndrome

A Phase 1 study, sponsored by Boston Children's Hospital.

Completed
Registry status
Phase 1
Development phase
23
Enrollment target

NCT00272844: Completed Phase 1 study, sponsored by Boston Children's Hospital.

NCT00272844 is a Phase 1 study that has completed, run by Boston Children's Hospital. The registered enrollment target is 23 participants, below the 60-participant average among 29,502 other Phase 1 trials with a reported enrollment target (62% lower). According to ClinicalTrials.gov, the official US trial registry.

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The verdict

NCT00272844, a Phase 1 study, has completed, sponsored by Boston Children's Hospital.

COMPLETED
Registry status
Phase 1
Development phase
23 participants
Enrollment target

Study Summary

The purpose of this study is to determine whether supplementation with an oil-based cholesterol suspension will correct the biochemical abnormalities in cholesterol and its precursors in individuals with the Smith-Lemli-Opitz syndrome.

Primary Outcome

Responders was defined as an increase in total serum cholesterol and a decrease in 7-DHC (7-Dehydrocholesterol), and 8-DHC (8-Dehydrocholesterol) were measured on all participants.

Interventions

  • DRUG crystalline cholesterol oil-based suspension

Trial Details

FieldValue
Enrollment Target 23 participants
Start Date 1998-01
Est. Completion 2011-07
Phase Phase 1
Boston Children's Hospital

462 total trials

What the finished NCT00272844 record still lists

NCT00272844 is an interventional study that assigns participants to a tested intervention. The registry caps enrollment at 23 participants, a relatively small participant target, below the 60-participant average among 29,502 other Phase 1 trials with a reported enrollment target (62% lower).

The record links to 0 conditions, and to 1 intervention - of which crystalline cholesterol oil-based suspension is the first listed.

NCT00272844 does not publish any study locations in the registry export this page uses.

Frequently Asked Questions

What is clinical trial NCT00272844 about?

NCT00272844 is a clinical study titled "Treatment of the Cholesterol Defect in Smith-Lemli-Opitz Syndrome". The purpose of this study is to determine whether supplementation with an oil-based cholesterol suspension will correct the biochemical abnormalities in cholesterol and its precursors in individuals with the Smith-Lemli-Opitz syndrome.

What is the current status of trial NCT00272844?

This trial is currently completed. It is a Phase 1 study. The enrollment target is 23 participants. The study started on 1998-01. Estimated completion is 2011-07.

What interventions are being tested in trial NCT00272844?

The interventions under investigation include: crystalline cholesterol oil-based suspension (DRUG).

Who is sponsoring clinical trial NCT00272844?

This trial is sponsored by Boston Children's Hospital, which has 462 total clinical trials registered on ClinicalTrials.gov.

How this trial's enrollment target compares

Where NCT00272844's enrollment target sits among peer trials

23 1596th of 2000 higher than 400 of 2,000 other Phase 1 trials

participants (enrollment target), bucketed by value

Each bar is a band; taller bars hold more other Phase 1 trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.

Source ClinicalTrials.gov registry export · 2026-08-08

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Source: ClinicalTrials.gov NCT00272844, the US trial registry maintained by the National Library of Medicine. NCT00272844 (small enrollment · none site footprint · completed) retrieved and formatted by PlainTrial, see methodology.