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NCT00004378 · ClinicalTrials.gov registry record · NA
Stem Cell Transplantation (SCT) for Genetic Diseases
A NA study of Thrombocytopenia and Inborn Errors of Metabolism, sponsored by National Center for Research Resources (NCRR).
- Completed
- Registry status
- NA
- Development phase
- 1
- Study location
NCT00004378: Completed NA study of Thrombocytopenia and Inborn Errors of Metabolism, sponsored by National Center for Research Resources (NCRR).
NCT00004378 is a NA study of Thrombocytopenia and Inborn Errors of Metabolism that has completed, run by National Center for Research Resources (NCRR). The trial reports 1 study location across 1 state. According to ClinicalTrials.gov, the official US trial registry.
The verdict
NCT00004378, a NA study of Thrombocytopenia and Inborn Errors of Metabolism, has completed, sponsored by National Center for Research Resources (NCRR).
- COMPLETED
- Registry status
- NA
- Development phase
- 1
- Study location
Study Summary
OBJECTIVES: I. Ascertain whether stem cell transplantation (SCT) is an effective method by which missing or dysfunctional enzymes can be replaced in patients with various inborn errors of metabolism. II. Determine whether clinical manifestations of the specific disease may be arrested or reversed by this treatment.
Conditions Studied
Interventions
- PROCEDURE Stem Cell Transplantation
Study Locations (1)
California
- University of California Los Angeles Medical Center - Los Angeles
Trial Details
| Field | Value |
|---|---|
| Start Date | 1995-01 |
| Phase | NA |
What the finished NCT00004378 record still lists
NCT00004378 is an interventional study that assigns participants to a tested intervention. An enrollment target was not published in the registry record, which is common for early-stage or observational entries.
The record links to 6 conditions, with Thrombocytopenia appearing as the primary indexed condition, and to 1 intervention - of which Stem Cell Transplantation is the first listed.
NCT00004378 reports a single indexed study location in California.
Frequently Asked Questions
What is clinical trial NCT00004378 about?
NCT00004378 is a clinical study titled "Stem Cell Transplantation (SCT) for Genetic Diseases". OBJECTIVES: I. Ascertain whether stem cell transplantation (SCT) is an effective method by which missing or dysfunctional enzymes can be replaced in patients with various inborn errors of metabolism. II. Determine whether clinical manifestations of the specific disease may be arrested or reversed b...
What is the current status of trial NCT00004378?
This trial is currently completed. It is a NA study. The study started on 1995-01.
What conditions does trial NCT00004378 study?
This clinical trial studies the following conditions: Thrombocytopenia, Inborn Errors of Metabolism, Thalassemia Major, Metachromatic Leukodystrophy, Fanconi's Anemia.
What interventions are being tested in trial NCT00004378?
The interventions under investigation include: Stem Cell Transplantation (PROCEDURE).
Who is sponsoring clinical trial NCT00004378?
This trial is sponsored by National Center for Research Resources (NCRR), which has 94 total clinical trials registered on ClinicalTrials.gov.
Where is trial NCT00004378 being conducted?
This trial has 1 study location across California. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.
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