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NCT00004378 · ClinicalTrials.gov registry record · NA

Stem Cell Transplantation (SCT) for Genetic Diseases

A NA study of Thrombocytopenia and Inborn Errors of Metabolism, sponsored by National Center for Research Resources (NCRR).

Completed
Registry status
NA
Development phase
1
Study location

NCT00004378 is a NA study of Thrombocytopenia and Inborn Errors of Metabolism that has completed, run by National Center for Research Resources (NCRR). The trial reports 1 study location across 1 state.

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The verdict

NCT00004378, a NA study of Thrombocytopenia and Inborn Errors of Metabolism, has completed, sponsored by National Center for Research Resources (NCRR).

COMPLETED
Registry status
NA
Development phase
1
Study location

Study Summary

OBJECTIVES: I. Ascertain whether stem cell transplantation (SCT) is an effective method by which missing or dysfunctional enzymes can be replaced in patients with various inborn errors of metabolism. II. Determine whether clinical manifestations of the specific disease may be arrested or reversed by this treatment.

Interventions

  • PROCEDURE Stem Cell Transplantation

Study Locations (1)

California

  • University of California Los Angeles Medical Center - Los Angeles

Trial Details

FieldValue
Start Date 1995-01
Phase NA

What the Registry Record Tells You About NCT00004378

The ClinicalTrials.gov registry entry for NCT00004378 describes a study currently listed as completed, categorized as NA. An enrollment target was not published in the registry record, which is common for early-stage or observational entries. The listed sponsor is National Center for Research Resources (NCRR), which has 94 total studies on file at ClinicalTrials.gov.

The record links to 6 conditions, with Thrombocytopenia appearing as the primary indexed condition, and to 1 intervention - of which Stem Cell Transplantation is the first listed.

NCT00004378 reports 1 study location spanning 1 distinct geographic area - top geographies include California.

Frequently Asked Questions

What is clinical trial NCT00004378 about?

NCT00004378 is a clinical study titled "Stem Cell Transplantation (SCT) for Genetic Diseases". OBJECTIVES: I. Ascertain whether stem cell transplantation (SCT) is an effective method by which missing or dysfunctional enzymes can be replaced in patients with various inborn errors of metabolism. II. Determine whether clinical manifestations of the specific disease may be arrested or reversed b...

What is the current status of trial NCT00004378?

This trial is currently completed. It is a NA study. The study started on 1995-01.

What conditions does trial NCT00004378 study?

This clinical trial studies the following conditions: Thrombocytopenia, Inborn Errors of Metabolism, Thalassemia Major, Metachromatic Leukodystrophy, Fanconi's Anemia.

What interventions are being tested in trial NCT00004378?

The interventions under investigation include: Stem Cell Transplantation (PROCEDURE).

Who is sponsoring clinical trial NCT00004378?

This trial is sponsored by National Center for Research Resources (NCRR), which has 94 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT00004378 being conducted?

This trial has 1 study location across California. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

Data sourced from official public datasets. See our methodology for details. Retrieved and formatted by PlainTrial Editorial

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This page mirrors this trial's own ClinicalTrials.gov registry record, live from the dataset. See our editorial standards & corrections policy, the methodology behind these numbers, or report a data error.