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NCT06906367 · ClinicalTrials.gov registry record
A Study of Patients With Fabry Disease (US Specific)
A clinical trial of Fabry Disease, sponsored by Amicus Therapeutics.
- Recruiting
- Registry status
- 450
- Enrollment target
- 7
- Study locations
NCT06906367 is a study of Fabry Disease that is actively recruiting participants, run by Amicus Therapeutics. The registered enrollment target is 450 participants, below the 529-participant average among 32 other Fabry Disease trials with a reported enrollment target (15% lower). The trial reports 7 study locations across 7 states.
The verdict
NCT06906367, a study of Fabry Disease, is actively recruiting participants, sponsored by Amicus Therapeutics.
- RECRUITING
- Registry status
- 450 participants
- Enrollment target
- 7
- Study locations
Study Summary
This is an observational study to evaluate the effects of treatment on long-term effectiveness, safety, and health-related quality of life (HRQOL) in patients with Fabry disease, with a main focus on migalastat.
Conditions Studied
Interventions
- DRUG migalastat HCl
- DRUG ERT
Study Locations (7)
Alabama
- UAB Nephrology Research Clinic at Paula Building - Birmingham
Arkansas
- Arkansas Children's Hospital - Little Rock
Georgia
- Emory Genetics - Atlanta
Missouri
- Washington University School of Medicine - St Louis
Pennsylvania
- UPMC Children's Hospital of Pittsburgh - Pittsburgh
Texas
- Renal Disease Research Institute - Dallas
Virginia
- Lysosomal and Rare Disorders Research and Treatment Center, Inc. - Fairfax
Trial Details
| Field | Value |
|---|---|
| Enrollment Target | 450 participants |
| Start Date | 2026-02-13 |
| Est. Completion | 2032-06 |
Interested in This Trial?
Full Details on ClinicalTrials.gov ↗What the Registry Record Tells You About NCT06906367
The ClinicalTrials.gov registry entry for NCT06906367 describes a study currently listed as recruiting, categorized as an unspecified phase. The registered enrollment target is 450 participants, a figure that helps gauge the scale of data the investigators plan to collect, below the 529-participant average among 32 other Fabry Disease trials with a reported enrollment target (15% lower). The listed sponsor is Amicus Therapeutics, which has 34 total studies on file at ClinicalTrials.gov.
The record links to 1 condition, with Fabry Disease appearing as the primary indexed condition, and to 2 interventions - of which migalastat HCl is the first listed.
NCT06906367 reports 7 study locations spanning 7 distinct geographic areas - top geographies include Alabama, Arkansas, Georgia.
Frequently Asked Questions
What is clinical trial NCT06906367 about?
NCT06906367 is a clinical study titled "A Study of Patients With Fabry Disease (US Specific)". This is an observational study to evaluate the effects of treatment on long-term effectiveness, safety, and health-related quality of life (HRQOL) in patients with Fabry disease, with a main focus on migalastat.
What is the current status of trial NCT06906367?
This trial is currently recruiting. The enrollment target is 450 participants. The study started on 2026-02-13. Estimated completion is 2032-06.
What conditions does trial NCT06906367 study?
This clinical trial studies the following conditions: Fabry Disease.
What interventions are being tested in trial NCT06906367?
The interventions under investigation include: migalastat HCl (DRUG), ERT (DRUG).
Who is sponsoring clinical trial NCT06906367?
This trial is sponsored by Amicus Therapeutics, which has 34 total clinical trials registered on ClinicalTrials.gov.
Where is trial NCT06906367 being conducted?
This trial has 7 study locations across Alabama, Arkansas, Georgia, Missouri, Pennsylvania. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.
Learn More About Clinical Trials
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Read our methodology - how this data is sourced, computed, and verified.
Related
Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This page mirrors this trial's own ClinicalTrials.gov registry record, live from the dataset. See our editorial standards & corrections policy, the methodology behind these numbers, or report a data error.