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RECRUITING

A Study of Patients With Fabry Disease (US Specific)

NCT06906367 · View on ClinicalTrials.gov ↗

Study Summary

This is an observational study to evaluate the effects of treatment on long-term effectiveness, safety, and health-related quality of life (HRQOL) in patients with Fabry disease, with a main focus on migalastat.

Conditions Studied

Interventions

  • DRUG migalastat HCl
  • DRUG ERT

Study Locations (7)

Alabama

  • UAB Nephrology Research Clinic at Paula Building — Birmingham

Arkansas

  • Arkansas Children's Hospital — Little Rock

Georgia

  • Emory Genetics — Atlanta

Missouri

  • Washington University School of Medicine — St Louis

Pennsylvania

  • UPMC Children's Hospital of Pittsburgh — Pittsburgh

Texas

  • Renal Disease Research Institute — Dallas

Virginia

  • Lysosomal and Rare Disorders Research and Treatment Center, Inc. — Fairfax

Trial Details

FieldValue
Enrollment Target 450 participants
Start Date 2026-02-13
Est. Completion 2032-06

Sponsor

Amicus Therapeutics

14 total trials

Interested in This Trial?

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Full Details on ClinicalTrials.gov ↗

What the Registry Record Tells You About NCT06906367

The ClinicalTrials.gov registry entry for NCT06906367 describes a study currently listed as recruiting. It is categorized as an unspecified phase, which is the standard way researchers label where a study sits along the investigational pathway from early safety work through later efficacy and post-marketing evaluation. The registered enrollment target is 450 participants, a figure that helps gauge the scale of data the investigators plan to collect. The listed sponsor is Amicus Therapeutics, which has 14 total studies on file at ClinicalTrials.gov, and sponsors are the parties responsible for study design, oversight, and regulatory filings.

The record links to 1 condition, with Fabry Disease appearing as the primary indexed condition, and to 2 interventions — of which migalastat HCl is the first listed. Interventions can include drugs, devices, procedures, behavioral programs, or observational arms, and each is tracked as a separate registry field so that downstream queries can filter accurately. When a trial lists multiple interventions, it usually reflects a multi-arm design or a comparison protocol rather than a single treatment being tested in isolation. The brief summary published in the registry is the clearest source of protocol intent and should be read before drawing conclusions from any sidebar tags.

Geographic footprint matters for practical reasons: NCT06906367 reports 7 study locations spanning 7 distinct geographic areas — top geographies include Alabama, Arkansas, Georgia. A larger site network tends to correlate with broader recruitment capacity, but it does not imply anything about study quality, and site-level enrollment status can diverge from the overall registry status shown above. Every data point on this page comes from the public ClinicalTrials.gov dataset and is reproduced here for reference only; it is not a medical recommendation, an endorsement of the sponsor, or an invitation to enroll. Verify current status, eligibility criteria, and contact details directly at ClinicalTrials.gov, and discuss any participation decision with your own healthcare provider.

Frequently Asked Questions

What is clinical trial NCT06906367 about?

NCT06906367 is a clinical study titled "A Study of Patients With Fabry Disease (US Specific)". This is an observational study to evaluate the effects of treatment on long-term effectiveness, safety, and health-related quality of life (HRQOL) in patients with Fabry disease, with a main focus on migalastat.

What is the current status of trial NCT06906367?

This trial is currently recruiting. The enrollment target is 450 participants. The study started on 2026-02-13. Estimated completion is 2032-06.

What conditions does trial NCT06906367 study?

This clinical trial studies the following conditions: Fabry Disease. These conditions were identified from the trial registry and reflect the primary focus areas of the research.

What interventions are being tested in trial NCT06906367?

The interventions under investigation include: migalastat HCl (DRUG), ERT (DRUG). Each intervention is being evaluated for safety and efficacy as part of this clinical study.

Who is sponsoring clinical trial NCT06906367?

This trial is sponsored by Amicus Therapeutics, which has 14 total clinical trials registered on ClinicalTrials.gov. The sponsor is responsible for the study's design, funding, and regulatory compliance.

Where is trial NCT06906367 being conducted?

This trial has 7 study locations across Alabama, Arkansas, Georgia, Missouri, Pennsylvania. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

Related

Data sourced from official U.S. government datasets. See our methodology for details. Retrieved and formatted by PlainTrial Editorial