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NCT06817382 · ClinicalTrials.gov registry record · Phase 1

A Study to Investigate the Safety and Biodistribution of a Single Intrathecal (IT) Injection of INS1201 in Ambulatory Males With Duchenne Muscular Dystrophy (DMD)

A Phase 1 study of Duchenne Muscular Dystrophy, sponsored by Insmed Gene Therapy.

Recruiting
Registry status
Phase 1
Development phase
12
Enrollment target
9
Study locations

NCT06817382 is a Phase 1 study of Duchenne Muscular Dystrophy that is actively recruiting participants, run by Insmed Gene Therapy. The registered enrollment target is 12 participants, below the 412-participant average among 48 other Duchenne Muscular Dystrophy trials with a reported enrollment target (97% lower). The trial reports 9 study locations across 7 states.

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The verdict

NCT06817382, a Phase 1 study of Duchenne Muscular Dystrophy, is actively recruiting participants, sponsored by Insmed Gene Therapy.

RECRUITING
Registry status
Phase 1
Development phase
12 participants
Enrollment target
9
Study locations

Study Summary

The primary objective of this study is to evaluate the safety and tolerability of a single dose of INS1201 via IT administration in ambulatory male participants with DMD.

Interventions

  • GENETIC INS1201

Study Locations (9)

California

  • USA010 - Davis
  • USA002 - Palo Alto
  • USA005 - San Diego

Arkansas

  • USA012 - Little Rock

Georgia

  • Rare Disease Research (USA004) - Atlanta

New York

  • USA008 - Rochester

Ohio

  • USA006 - Columbus

Tennessee

  • USA001 - Memphis

Virginia

  • USA015 - Norfolk

Trial Details

FieldValue
Enrollment Target 12 participants
Start Date 2025-07-22
Est. Completion 2028-03-31
Phase Phase 1

Sponsor

Insmed Gene Therapy

2 total trials

What the Registry Record Tells You About NCT06817382

The ClinicalTrials.gov registry entry for NCT06817382 describes a study currently listed as recruiting, categorized as Phase 1. The registered enrollment target is 12 participants, a figure that helps gauge the scale of data the investigators plan to collect, below the 412-participant average among 48 other Duchenne Muscular Dystrophy trials with a reported enrollment target (97% lower). The listed sponsor is Insmed Gene Therapy, which has 2 total studies on file at ClinicalTrials.gov.

The record links to 1 condition, with Duchenne Muscular Dystrophy appearing as the primary indexed condition, and to 1 intervention - of which INS1201 is the first listed.

NCT06817382 reports 9 study locations spanning 7 distinct geographic areas - top geographies include California, Arkansas, Georgia.

Frequently Asked Questions

What is clinical trial NCT06817382 about?

NCT06817382 is a clinical study titled "A Study to Investigate the Safety and Biodistribution of a Single Intrathecal (IT) Injection of INS1201 in Ambulatory Males With Duchenne Muscular Dystrophy (DMD)". The primary objective of this study is to evaluate the safety and tolerability of a single dose of INS1201 via IT administration in ambulatory male participants with DMD.

What is the current status of trial NCT06817382?

This trial is currently recruiting. It is a Phase 1 study. The enrollment target is 12 participants. The study started on 2025-07-22. Estimated completion is 2028-03-31.

What conditions does trial NCT06817382 study?

This clinical trial studies the following conditions: Duchenne Muscular Dystrophy.

What interventions are being tested in trial NCT06817382?

The interventions under investigation include: INS1201 (GENETIC).

Who is sponsoring clinical trial NCT06817382?

This trial is sponsored by Insmed Gene Therapy, which has 2 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT06817382 being conducted?

This trial has 9 study locations across Arkansas, California, Georgia, New York, Ohio. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

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Data sourced from official public datasets. See our methodology for details. Retrieved and formatted by PlainTrial Editorial

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