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NCT05616793 · ClinicalTrials.gov registry record · Phase 1

Safety and Tolerability Subretinal OPGx-001 for LCA5-Associated Inherited Retinal Degeneration (LCA5-IRD) and Non-interventional Arm With Untreated Patients

A Phase 1 study of LCA5, sponsored by Opus Genetics.

Recruiting
Registry status
Phase 1
Development phase
22
Enrollment target
2
Study locations

NCT05616793 is a Phase 1 study of LCA5 that is actively recruiting participants, run by Opus Genetics. The registered enrollment target is 22 participants. The trial reports 2 study locations across 2 states.

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The verdict

NCT05616793, a Phase 1 study of LCA5, is actively recruiting participants, sponsored by Opus Genetics.

RECRUITING
Registry status
Phase 1
Development phase
22 participants
Enrollment target
2
Study locations

Study Summary

The goals of this clinical trial are assess the natural course of LCA5-IRD over 6 months and to evaluate the safety and preliminary efficacy of subretinal gene therapy with OPGx-001 in patients with inherited retinal degeneration due to biallelic mutations in the LCA5 gene. Funding Source- FDA Office of Orphan Products Development (OOPD).

Conditions Studied

Interventions

  • BIOLOGICAL AAV8.hLCA5

Study Locations (2)

Pennsylvania

  • University of Pennsylvania Perelman School of Medicine - Philadelphia

Texas

  • Retina Foundation of the Southwest - Dallas

Trial Details

FieldValue
Enrollment Target 22 participants
Start Date 2023-06-15
Est. Completion 2028-06-15
Phase Phase 1

Sponsor

Opus Genetics

3 total trials

What the Registry Record Tells You About NCT05616793

The ClinicalTrials.gov registry entry for NCT05616793 describes a study currently listed as recruiting, categorized as Phase 1. The registered enrollment target is 22 participants, a figure that helps gauge the scale of data the investigators plan to collect. The listed sponsor is Opus Genetics, which has 3 total studies on file at ClinicalTrials.gov.

The record links to 1 condition, with LCA5 appearing as the primary indexed condition, and to 1 intervention - of which AAV8.hLCA5 is the first listed.

NCT05616793 reports 2 study locations spanning 2 distinct geographic areas - top geographies include Pennsylvania, Texas.

Frequently Asked Questions

What is clinical trial NCT05616793 about?

NCT05616793 is a clinical study titled "Safety and Tolerability Subretinal OPGx-001 for LCA5-Associated Inherited Retinal Degeneration (LCA5-IRD) and Non-interventional Arm With Untreated Patients". The goals of this clinical trial are assess the natural course of LCA5-IRD over 6 months and to evaluate the safety and preliminary efficacy of subretinal gene therapy with OPGx-001 in patients with inherited retinal degeneration due to biallelic mutations in the LCA5 gene. Funding Source- FDA Offic...

What is the current status of trial NCT05616793?

This trial is currently recruiting. It is a Phase 1 study. The enrollment target is 22 participants. The study started on 2023-06-15. Estimated completion is 2028-06-15.

What conditions does trial NCT05616793 study?

This clinical trial studies the following conditions: LCA5.

What interventions are being tested in trial NCT05616793?

The interventions under investigation include: AAV8.hLCA5 (BIOLOGICAL).

Who is sponsoring clinical trial NCT05616793?

This trial is sponsored by Opus Genetics, which has 3 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT05616793 being conducted?

This trial has 2 study locations across Pennsylvania, Texas. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

Data sourced from official public datasets. See our methodology for details. Retrieved and formatted by PlainTrial Editorial

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This page mirrors this trial's own ClinicalTrials.gov registry record, live from the dataset. See our editorial standards & corrections policy, the methodology behind these numbers, or report a data error.