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NCT02407080 · ClinicalTrials.gov registry record · Phase 1

Open Label Study of Single Agent Oral RG7388 in Patients With Polycythemia Vera and Essential Thrombocythemia

A Phase 1 study, sponsored by John Mascarenhas.

Completed
Registry status
Phase 1
Development phase
13
Enrollment target

NCT02407080: Completed Phase 1 study, sponsored by John Mascarenhas.

NCT02407080 is a Phase 1 study that has completed, run by John Mascarenhas. The registered enrollment target is 13 participants, below the 60-participant average among 29,502 other Phase 1 trials with a reported enrollment target (78% lower). According to ClinicalTrials.gov, the official US trial registry.

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The verdict

NCT02407080, a Phase 1 study, has completed, sponsored by John Mascarenhas.

COMPLETED
Registry status
Phase 1
Development phase
13 participants
Enrollment target

Study Summary

This research looks at two conditions, Essential Thrombocythemia (ET) and Polycythemia Vera (PV). ET causes people to produce too many blood cells called platelets and PV causes too many platelets and red blood cells to be made. Platelets are particles which circulate in the blood stream and normally prevent bleeding and bruising. Having too many platelets in the blood increases the risk of developing blood clots, which can result in life threatening events like heart attacks and strokes. When the number of red blood cells is increased in PV this will slow the speed of blood flow in the body and increase the risk of developing blood clots. The purpose of Part A of this study is to test the safety and tolerability of drug RG7388 patients and identify the recommended phase II dose in a single agent dose escalation study. The investigators want to find out what effects, good and/or bad it has on the disease. The purpose of Part B of this study is to test the safety and tolerability of the combination of RG7388 and Pegylated Interferon Alfa-2a or Pegasys in PV/ET patients from Part A who did not achieve at least a partial response by the end of three cycles of single agent RG7388. Essential Thrombocythemia (ET) and Polycythemia Vera (PV) have been difficult diseases to treat. RG7388 is a selective inhibitor of the p53-MDM2 binding that frees p53 from negative control and activates the p53 pathway in cancer cells, leading to cell cycle arrest and apoptosis in vitro and in vivo. It has been used to treat solid tumors and Acute Myelogenous Leukemia (AML) in clinical trials. Pegasys is a drug that is the standard of care for patients who have Chronic Hepatitis B (CHB). RG7388 is a drug that is not yet approved by the Federal Drug Administration (FDA) for the treatment of patients with essential thrombocythemia or polycythemia vera. Pegasys is a drug that is approved by the FDA for the treatment of CHB. The use of RG7388 alone and in combination with Pegasys is experimen

Interventions

  • DRUG Pegasys
  • DRUG RG7388

Trial Details

FieldValue
Enrollment Target 13 participants
Start Date 2015-04
Est. Completion 2018-12-19
Phase Phase 1
John Mascarenhas

11 total trials

What the finished NCT02407080 record still lists

NCT02407080 is an interventional study that assigns participants to a tested intervention. The registry caps enrollment at 13 participants, a relatively small participant target, below the 60-participant average among 29,502 other Phase 1 trials with a reported enrollment target (78% lower).

The record links to 0 conditions, and to 2 interventions - of which Pegasys is the first listed.

NCT02407080 does not publish any study locations in the registry export this page uses.

Frequently Asked Questions

What is clinical trial NCT02407080 about?

NCT02407080 is a clinical study titled "Open Label Study of Single Agent Oral RG7388 in Patients With Polycythemia Vera and Essential Thrombocythemia". This research looks at two conditions, Essential Thrombocythemia (ET) and Polycythemia Vera (PV). ET causes people to produce too many blood cells called platelets and PV causes too many platelets and red blood cells to be made. Platelets are particles which circulate in the blood stream and normall...

What is the current status of trial NCT02407080?

This trial is currently completed. It is a Phase 1 study. The enrollment target is 13 participants. The study started on 2015-04. Estimated completion is 2018-12-19.

What interventions are being tested in trial NCT02407080?

The interventions under investigation include: Pegasys (DRUG), RG7388 (DRUG).

Who is sponsoring clinical trial NCT02407080?

This trial is sponsored by John Mascarenhas, which has 11 total clinical trials registered on ClinicalTrials.gov.

How this trial's enrollment target compares

Where NCT02407080's enrollment target sits among peer trials

13 1847th of 2000 higher than 149 of 2,000 other Phase 1 trials

participants (enrollment target), bucketed by value

Each bar is a band; taller bars hold more other Phase 1 trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.

Source ClinicalTrials.gov registry export · 2026-08-08

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Source: ClinicalTrials.gov NCT02407080, the US trial registry maintained by the National Library of Medicine. NCT02407080 (small enrollment · none site footprint · completed) retrieved and formatted by PlainTrial, see methodology.