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NCT02295748 · ClinicalTrials.gov registry record · Phase 1

An Open-Label, Long-Term Extension Study to Evaluate the Safety and Tolerability Deflazacort

A Phase 1 study, sponsored by PTC Therapeutics.

Completed
Registry status
Phase 1
Development phase
24
Enrollment target

NCT02295748: Completed Phase 1 study, sponsored by PTC Therapeutics.

NCT02295748 is a Phase 1 study that has completed, run by PTC Therapeutics. The registered enrollment target is 24 participants, below the 60-participant average among 29,502 other Phase 1 trials with a reported enrollment target (60% lower). According to ClinicalTrials.gov, the official US trial registry.

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The verdict

NCT02295748, a Phase 1 study, has completed, sponsored by PTC Therapeutics.

COMPLETED
Registry status
Phase 1
Development phase
24 participants
Enrollment target

Study Summary

This is an open label, long-term extension study in approximately 24 male DMD subjects consisting of children (ages 4-12, inclusive) and adolescents (ages 13-16, inclusive) who participated in the MP-104-CL-005 PK study.

Primary Outcome

Long-term safety and tolerability will be characterized by the number, frequency, and severity of adverse events from Day 1 through End of Study or Early Termination.

Interventions

  • DRUG Deflazacort

Trial Details

FieldValue
Enrollment Target 24 participants
Start Date 2014-12
Est. Completion 2017-08-24
Phase Phase 1
PTC Therapeutics

52 total trials

What the finished NCT02295748 record still lists

NCT02295748 is an interventional study that assigns participants to a tested intervention. The registry caps enrollment at 24 participants, a relatively small participant target, below the 60-participant average among 29,502 other Phase 1 trials with a reported enrollment target (60% lower).

The record links to 0 conditions, and to 1 intervention - of which Deflazacort is the first listed.

NCT02295748 does not publish any study locations in the registry export this page uses.

Frequently Asked Questions

What is clinical trial NCT02295748 about?

NCT02295748 is a clinical study titled "An Open-Label, Long-Term Extension Study to Evaluate the Safety and Tolerability Deflazacort". This is an open label, long-term extension study in approximately 24 male DMD subjects consisting of children (ages 4-12, inclusive) and adolescents (ages 13-16, inclusive) who participated in the MP-104-CL-005 PK study.

What is the current status of trial NCT02295748?

This trial is currently completed. It is a Phase 1 study. The enrollment target is 24 participants. The study started on 2014-12. Estimated completion is 2017-08-24.

What interventions are being tested in trial NCT02295748?

The interventions under investigation include: Deflazacort (DRUG).

Who is sponsoring clinical trial NCT02295748?

This trial is sponsored by PTC Therapeutics, which has 52 total clinical trials registered on ClinicalTrials.gov.

How this trial's enrollment target compares

Where NCT02295748's enrollment target sits among peer trials

24 1520th of 2000 higher than 405 of 2,000 other Phase 1 trials

participants (enrollment target), bucketed by value

Each bar is a band; taller bars hold more other Phase 1 trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.

Source ClinicalTrials.gov registry export · 2026-08-08

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Source: ClinicalTrials.gov NCT02295748, the US trial registry maintained by the National Library of Medicine. NCT02295748 (small enrollment · none site footprint · completed) retrieved and formatted by PlainTrial, see methodology.