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NCT02251600 · ClinicalTrials.gov registry record · Phase 1
A Pharmacokinetic Study of Oral Deflazacort in Children and Adolescent Subjects With Duchenne Muscular Dystrophy
A Phase 1 study, sponsored by PTC Therapeutics.
- Completed
- Registry status
- Phase 1
- Development phase
- 24
- Enrollment target
NCT02251600: Completed Phase 1 study, sponsored by PTC Therapeutics.
NCT02251600 is a Phase 1 study that has completed, run by PTC Therapeutics. The registered enrollment target is 24 participants, below the 60-participant average among 29,502 other Phase 1 trials with a reported enrollment target (60% lower). According to ClinicalTrials.gov, the official US trial registry.
The verdict
NCT02251600, a Phase 1 study, has completed, sponsored by PTC Therapeutics.
- COMPLETED
- Registry status
- Phase 1
- Development phase
- 24 participants
- Enrollment target
Study Summary
Study to characterize the single-state and steady-state dosing of oral deflazacort in pediatric and adolescents subjects.
Primary Outcome
The area under the plasma concentration time curve, from time 0 to the last measurable concentration non-zero, for single-state pharmacokinetics on Day 1 of deflazacort and 21-desacetyl-DFZ, the active metabolite
Interventions
- DRUG Deflazacort
Trial Details
| Field | Value |
|---|---|
| Enrollment Target | 24 participants |
| Start Date | 2014-12 |
| Est. Completion | 2015-10 |
| Phase | Phase 1 |
What the finished NCT02251600 record still lists
NCT02251600 is an interventional study that assigns participants to a tested intervention. The registry caps enrollment at 24 participants, a relatively small participant target, below the 60-participant average among 29,502 other Phase 1 trials with a reported enrollment target (60% lower).
The record links to 0 conditions, and to 1 intervention - of which Deflazacort is the first listed.
NCT02251600 does not publish any study locations in the registry export this page uses.
Frequently Asked Questions
What is clinical trial NCT02251600 about?
NCT02251600 is a clinical study titled "A Pharmacokinetic Study of Oral Deflazacort in Children and Adolescent Subjects With Duchenne Muscular Dystrophy". Study to characterize the single-state and steady-state dosing of oral deflazacort in pediatric and adolescents subjects.
What is the current status of trial NCT02251600?
This trial is currently completed. It is a Phase 1 study. The enrollment target is 24 participants. The study started on 2014-12. Estimated completion is 2015-10.
What interventions are being tested in trial NCT02251600?
The interventions under investigation include: Deflazacort (DRUG).
Who is sponsoring clinical trial NCT02251600?
This trial is sponsored by PTC Therapeutics, which has 52 total clinical trials registered on ClinicalTrials.gov.
Learn More About Clinical Trials
How this trial's enrollment target compares
Where NCT02251600's enrollment target sits among peer trials
24 1520th of 2000 higher than 405 of 2,000 other Phase 1 trials
participants (enrollment target), bucketed by value
Each bar is a band; taller bars hold more other Phase 1 trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.
Source ClinicalTrials.gov registry export · 2026-08-08
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