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NCT02231697 · ClinicalTrials.gov registry record
A Medical Chart Review of Patients With X-Linked Myotubular Myopathy (XLMTM)
A clinical trial, sponsored by Astellas Gene Therapies.
- Completed
- Registry status
- 161
- Enrollment target
NCT02231697: Completed study, sponsored by Astellas Gene Therapies.
NCT02231697 is a clinical trial that has completed, run by Astellas Gene Therapies. The registered enrollment target is 161 participants. According to ClinicalTrials.gov, the official US trial registry.
The verdict
NCT02231697 has completed, sponsored by Astellas Gene Therapies.
- COMPLETED
- Registry status
- 161 participants
- Enrollment target
Study Summary
This retrospective medical chart review (RECENSUS) of approximately 100 XLMTM patients (with a goal to obtain 50 deceased and 20 living records) will provide further knowledge about the clinical manifestations and recorded medical management of XLMTM and potentially inform the design of future therapeutic intervention studies.
Primary Outcome
Descriptive statistics: mean, median, range for age at death for deceased patients, mean, median, range for current age for living patients
Interventions
- OTHER Non-interventional, retrospective medical chart review
Trial Details
| Field | Value |
|---|---|
| Enrollment Target | 161 participants |
| Start Date | 2014-09 |
| Est. Completion | 2019-12 |
What the finished NCT02231697 record still lists
NCT02231697 is an observational study that tracks outcomes without assigning an intervention. The registered 161 participants enrollment target is mid-sized for trials with a published cap.
The record links to 0 conditions, and to 1 intervention - of which Non-interventional, retrospective medical chart review is the first listed.
NCT02231697 does not publish any study locations in the registry export this page uses.
Frequently Asked Questions
What is clinical trial NCT02231697 about?
NCT02231697 is a clinical study titled "A Medical Chart Review of Patients With X-Linked Myotubular Myopathy (XLMTM)". This retrospective medical chart review (RECENSUS) of approximately 100 XLMTM patients (with a goal to obtain 50 deceased and 20 living records) will provide further knowledge about the clinical manifestations and recorded medical management of XLMTM and potentially inform the design of future thera...
What is the current status of trial NCT02231697?
This trial is currently completed. The enrollment target is 161 participants. The study started on 2014-09. Estimated completion is 2019-12.
What interventions are being tested in trial NCT02231697?
The interventions under investigation include: Non-interventional, retrospective medical chart review (OTHER).
Who is sponsoring clinical trial NCT02231697?
This trial is sponsored by Astellas Gene Therapies, which has 7 total clinical trials registered on ClinicalTrials.gov.
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