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NCT02053480 · ClinicalTrials.gov registry record
Pyruvate Kinase Deficiency Natural History Study
A clinical trial of Pyruvate Kinase Deficiency and Congenital Non-Spherocytic Hemolytic Anemia, sponsored by Boston Children's Hospital.
- Completed
- Registry status
- 254
- Enrollment target
- 20
- Study locations
NCT02053480: Completed study of Pyruvate Kinase Deficiency and Congenital Non-Spherocytic Hemolytic Anemia, sponsored by Boston Children's Hospital.
NCT02053480 is a study of Pyruvate Kinase Deficiency and Congenital Non-Spherocytic Hemolytic Anemia that has completed, run by Boston Children's Hospital. The registered enrollment target is 254 participants. The trial reports 20 study locations across 17 states. According to ClinicalTrials.gov, the official US trial registry.
The verdict
NCT02053480, a study of Pyruvate Kinase Deficiency and Congenital Non-Spherocytic Hemolytic Anemia, has completed, sponsored by Boston Children's Hospital.
- COMPLETED
- Registry status
- 254 participants
- Enrollment target
- 20
- Study locations
Study Summary
The purpose of this study is to describe the range and incidence of symptoms, treatments, and complications related to pyruvate kinase deficiency (PKD). Eligible patients are those of all ages with known PKD or with a hemolytic anemia and a family member with PKD. The study will collect retrospective medical history, routine clinical care data, and quality of life measures at baseline and annually for patients with PKD.
Conditions Studied
Study Locations (20)
Massachusetts
- Boston Children's Hospital - Boston
- University of Massachusetts Medical Center - Worcester
Ohio
- Nationwide Children's Hospital - Columbus
- DDC Clinic for Special Needs Children - Middlefield
Pennsylvania
- Children's Hospital of Philadelphia - Philadelphia
- Central Pennsylvania Clinic - Strasburg
Arizona
- Phoenix Children's Hospital - Phoenix
California
- Stanford University - Palo Alto
Georgia
- Children's Hospital of Atlanta - Atlanta
Illinois
- Lurie Children's Hospital - Chicago
Michigan
- Wayne State University School of Medicine - Detroit
Trial Details
| Field | Value |
|---|---|
| Enrollment Target | 254 participants |
| Start Date | 2013-12 |
| Est. Completion | 2020-05 |
What the finished NCT02053480 record still lists
NCT02053480 is an observational study that tracks outcomes without assigning an intervention. The registered 254 participants enrollment target is mid-sized for trials with a published cap.
The record links to 2 conditions, with Pyruvate Kinase Deficiency appearing as the primary indexed condition, and to 0 interventions.
NCT02053480 names 20 study sites across 17 states, led by Massachusetts, Ohio, Pennsylvania.
Frequently Asked Questions
What is clinical trial NCT02053480 about?
NCT02053480 is a clinical study titled "Pyruvate Kinase Deficiency Natural History Study". The purpose of this study is to describe the range and incidence of symptoms, treatments, and complications related to pyruvate kinase deficiency (PKD). Eligible patients are those of all ages with known PKD or with a hemolytic anemia and a family member with PKD. The study will collect retrospectiv...
What is the current status of trial NCT02053480?
This trial is currently completed. The enrollment target is 254 participants. The study started on 2013-12. Estimated completion is 2020-05.
What conditions does trial NCT02053480 study?
This clinical trial studies the following conditions: Pyruvate Kinase Deficiency, Congenital Non-Spherocytic Hemolytic Anemia.
Who is sponsoring clinical trial NCT02053480?
This trial is sponsored by Boston Children's Hospital, which has 462 total clinical trials registered on ClinicalTrials.gov.
Where is trial NCT02053480 being conducted?
This trial has 20 study locations across Arizona, California, Georgia, Illinois, Massachusetts. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.
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