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NCT01884220 · ClinicalTrials.gov registry record
Wolman/CESD Natural History Chart Review and Longitudinal Follow-Up
A clinical trial, sponsored by Children's Hospital Medical Center, Cincinnati.
- Completed
- Registry status
- 4
- Enrollment target
NCT01884220: Completed study, sponsored by Children's Hospital Medical Center, Cincinnati.
NCT01884220 is a clinical trial that has completed, run by Children's Hospital Medical Center, Cincinnati. The registered enrollment target is 4 participants. According to ClinicalTrials.gov, the official US trial registry.
The verdict
NCT01884220 has completed, sponsored by Children's Hospital Medical Center, Cincinnati.
- COMPLETED
- Registry status
- 4 participants
- Enrollment target
Study Summary
The purpose of this study are: to characterize and understand the natural history of disease progression in WD and CESD, and to provide historical controls for WD and CESD for developing clinical treatment trials. The hypothesis is that the variability and clinical progression in WD and CESD is large and represents a continuum of severities from a lethal infantile to near normal adults with only "fatty livers".
Primary Outcome
Measurement of the effect over time of LAL deficiency on the liver, spleen, intestines, lungs and adrenals will be performed using ultrasound imaging. Measurement using ultrasound imaging will only be completed if clinically indicated during clinical-care patient visits.
Interventions
- OTHER There are no interventions in this study.
Trial Details
| Field | Value |
|---|---|
| Enrollment Target | 4 participants |
| Start Date | 2010-11 |
| Est. Completion | 2014-05 |
What the finished NCT01884220 record still lists
NCT01884220 is an observational study that tracks outcomes without assigning an intervention. The registry caps enrollment at 4 participants, a relatively small participant target.
The record links to 0 conditions, and to 1 intervention - of which There are no interventions in this study. is the first listed.
NCT01884220 does not publish any study locations in the registry export this page uses.
Frequently Asked Questions
What is clinical trial NCT01884220 about?
NCT01884220 is a clinical study titled "Wolman/CESD Natural History Chart Review and Longitudinal Follow-Up". The purpose of this study are: to characterize and understand the natural history of disease progression in WD and CESD, and to provide historical controls for WD and CESD for developing clinical treatment trials. The hypothesis is that the variability and clinical progression in WD and CESD is larg...
What is the current status of trial NCT01884220?
This trial is currently completed. The enrollment target is 4 participants. The study started on 2010-11. Estimated completion is 2014-05.
What interventions are being tested in trial NCT01884220?
The interventions under investigation include: There are no interventions in this study. (OTHER).
Who is sponsoring clinical trial NCT01884220?
This trial is sponsored by Children's Hospital Medical Center, Cincinnati, which has 571 total clinical trials registered on ClinicalTrials.gov.
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