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NCT01703169 · ClinicalTrials.gov registry record · Phase 2

Efficacy and Safety of Eltrombopag In Patients With Severe and Very Severe Aplastic Anemia

A Phase 2 study, sponsored by University of Utah.

Completed
Registry status
Phase 2
Development phase
13
Enrollment target

NCT01703169: Completed Phase 2 study, sponsored by University of Utah.

NCT01703169 is a Phase 2 study that has completed, run by University of Utah. The registered enrollment target is 13 participants, below the 133-participant average among 30,622 other Phase 2 trials with a reported enrollment target (90% lower). According to ClinicalTrials.gov, the official US trial registry.

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The verdict

NCT01703169, a Phase 2 study, has completed, sponsored by University of Utah.

COMPLETED
Registry status
Phase 2
Development phase
13 participants
Enrollment target

Study Summary

The investigators hypothesis is that eltrombopag given to patients with moderate to very severe aplastic anemia will result in an increase in platelet counts. The investigators hypothesize that in patients with moderate to very severe aplastic anemia, treatment with eltrombopag will lead to fewer platelet transfusions, red blood cell transfusions, and fewer bleeding events. The investigators hypothesize that in patients with moderate to very severe aplastic anemia, eltrombopag will have an acceptable toxicity rate \<3%, at doses that result in increased platelet counts. Finally the investigators hypothesize that plasma eltrombopag levels in peripheral blood will correlate with improved platelet counts.

Primary Outcome

Defined as a stable platelet count of 50,000/μl or more during any 4 week period within the possible 12 weeks while on study,and including maximal platelet counts achieved in patients with moderate to very severe aplastic anemia.

Interventions

  • DRUG Eltrombopag

Trial Details

FieldValue
Enrollment Target 13 participants
Start Date 2012-11
Est. Completion 2016-06
Phase Phase 2
University of Utah

818 total trials

What the finished NCT01703169 record still lists

NCT01703169 is an interventional study that assigns participants to a tested intervention. The registry caps enrollment at 13 participants, a relatively small participant target, below the 133-participant average among 30,622 other Phase 2 trials with a reported enrollment target (90% lower).

The record links to 0 conditions, and to 1 intervention - of which Eltrombopag is the first listed.

NCT01703169 does not publish any study locations in the registry export this page uses.

Frequently Asked Questions

What is clinical trial NCT01703169 about?

NCT01703169 is a clinical study titled "Efficacy and Safety of Eltrombopag In Patients With Severe and Very Severe Aplastic Anemia". The investigators hypothesis is that eltrombopag given to patients with moderate to very severe aplastic anemia will result in an increase in platelet counts. The investigators hypothesize that in patients with moderate to very severe aplastic anemia, treatment with eltrombopag will lead to fewer pl...

What is the current status of trial NCT01703169?

This trial is currently completed. It is a Phase 2 study. The enrollment target is 13 participants. The study started on 2012-11. Estimated completion is 2016-06.

What interventions are being tested in trial NCT01703169?

The interventions under investigation include: Eltrombopag (DRUG).

Who is sponsoring clinical trial NCT01703169?

This trial is sponsored by University of Utah, which has 818 total clinical trials registered on ClinicalTrials.gov.

How this trial's enrollment target compares

Where NCT01703169's enrollment target sits among peer trials

13 1947th of 2000 higher than 53 of 2,000 other Phase 2 trials

participants (enrollment target), bucketed by value

Each bar is a band; taller bars hold more other Phase 2 trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.

Source ClinicalTrials.gov registry export · 2026-08-08

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Source: ClinicalTrials.gov NCT01703169, the US trial registry maintained by the National Library of Medicine. NCT01703169 (small enrollment · none site footprint · completed) retrieved and formatted by PlainTrial, see methodology.