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NCT01419028 · ClinicalTrials.gov registry record
A Retrospective Study of the Natural History of Patients With Severe Perinatal and Infantile Hypophosphatasia (HPP)
A clinical trial of Hypophosphatasia (HPP), sponsored by Alexion Pharmaceuticals.
- Completed
- Registry status
- 48
- Enrollment target
- 12
- Study locations
NCT01419028: Completed study of Hypophosphatasia (HPP), sponsored by Alexion Pharmaceuticals.
NCT01419028 is a study of Hypophosphatasia (HPP) that has completed, run by Alexion Pharmaceuticals. The registered enrollment target is 48 participants. The trial reports 12 study locations across 6 states. According to ClinicalTrials.gov, the official US trial registry.
The verdict
NCT01419028, a study of Hypophosphatasia (HPP), has completed, sponsored by Alexion Pharmaceuticals.
- COMPLETED
- Registry status
- 48 participants
- Enrollment target
- 12
- Study locations
Study Summary
This study aims to characterize the natural history of patients with severe perinatal or infantile onset HPP.
Primary Outcome
Overall survival is defined as the time from birth to time of death.
Conditions Studied
Study Locations (12)
Other
- Royal Children's Hospital - Parkville
- University of Manitoba Health Sciences Centre - Winnipeg
- Universitatsmedizin Mainz, Villa - Mainz
- Universitätsklinikum Würzburg Kinderklinik, Pädiatrische Infektiologie und Immunologie - Würzburg
- Hospital Infantil Universitario Nino Jesus Universidad autonoma de Madrid - Madrid
- National Taiwan University Hospital - Taipei
- Birmingham Childrens Hospital - Birmingham
California
- Cedars-Sinai Medical Center - Los Angeles
Indiana
- Indiana University school of medicine - Indianapolis
Missouri
- Shriners Hospital for Children - St Louis
Oregon
- Oregon Health & Science University - Portland
Texas
- Cook Children's Health Care System - Fort Worth
Trial Details
| Field | Value |
|---|---|
| Enrollment Target | 48 participants |
| Start Date | 2012-08 |
| Est. Completion | 2014-02 |
What the finished NCT01419028 record still lists
NCT01419028 is an observational study that tracks outcomes without assigning an intervention. The registry caps enrollment at 48 participants, a relatively small participant target.
The record links to 1 condition, with Hypophosphatasia (HPP) appearing as the primary indexed condition, and to 0 interventions.
NCT01419028 lists 12 locations in 6 states (Other, California, Indiana).
Frequently Asked Questions
What is clinical trial NCT01419028 about?
NCT01419028 is a clinical study titled "A Retrospective Study of the Natural History of Patients With Severe Perinatal and Infantile Hypophosphatasia (HPP)". This study aims to characterize the natural history of patients with severe perinatal or infantile onset HPP.
What is the current status of trial NCT01419028?
This trial is currently completed. The enrollment target is 48 participants. The study started on 2012-08. Estimated completion is 2014-02.
What conditions does trial NCT01419028 study?
This clinical trial studies the following conditions: Hypophosphatasia (HPP).
Who is sponsoring clinical trial NCT01419028?
This trial is sponsored by Alexion Pharmaceuticals, which has 162 total clinical trials registered on ClinicalTrials.gov.
Where is trial NCT01419028 being conducted?
This trial has 12 study locations across California, Indiana, Missouri, Oregon, Texas. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.
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