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NCT01369160 · ClinicalTrials.gov registry record
Curative Versus Disease-Modifying Therapies in Children With Severe Sickle Cell Disease
A clinical trial, sponsored by Emory University.
- Completed
- Registry status
- 33
- Enrollment target
NCT01369160 is a clinical trial that has completed, run by Emory University. The registered enrollment target is 33 participants.
The verdict
NCT01369160 has completed, sponsored by Emory University.
- COMPLETED
- Registry status
- 33 participants
- Enrollment target
Study Summary
The research proposed is a pilot study of pediatric and adolescent/young adult patients who have received the curative intervention (MSD-SCT), disease-modifying interventions (HU or CT) or SCC (control), with respect to three clinically important outcomes: quality-of-life (QOL), neurocognitive function, and reproductive potential. Comparable cohorts will be identified for each of the groups, drawing from patients treated by the SCD program of Children's Healthcare of Atlanta (CHOA). QOL measures and neuropsychiatric testing and will be administered. Reproductive endocrine function markers (laboratory studies and pubertal staging), will be collected and analyzed. A tracking system of such patients will also be developed, gathering available retrospective data and setting up a mechanism for collection of new data.
Interventions
- BEHAVIORAL Quality of Life measures
Trial Details
| Field | Value |
|---|---|
| Enrollment Target | 33 participants |
| Start Date | 2005-05 |
| Est. Completion | 2014-03 |
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Full Details on ClinicalTrials.gov ↗What the Registry Record Tells You About NCT01369160
The ClinicalTrials.gov registry entry for NCT01369160 describes a study currently listed as completed, categorized as an unspecified phase. The registered enrollment target is 33 participants, a figure that helps gauge the scale of data the investigators plan to collect. The listed sponsor is Emory University, which has 1,208 total studies on file at ClinicalTrials.gov.
The record links to 0 conditions, and to 1 intervention - of which Quality of Life measures is the first listed.
NCT01369160 reports 0 study locations.
Frequently Asked Questions
What is clinical trial NCT01369160 about?
NCT01369160 is a clinical study titled "Curative Versus Disease-Modifying Therapies in Children With Severe Sickle Cell Disease". The research proposed is a pilot study of pediatric and adolescent/young adult patients who have received the curative intervention (MSD-SCT), disease-modifying interventions (HU or CT) or SCC (control), with respect to three clinically important outcomes: quality-of-life (QOL), neurocognitive funct...
What is the current status of trial NCT01369160?
This trial is currently completed. The enrollment target is 33 participants. The study started on 2005-05. Estimated completion is 2014-03.
What interventions are being tested in trial NCT01369160?
The interventions under investigation include: Quality of Life measures (BEHAVIORAL).
Who is sponsoring clinical trial NCT01369160?
This trial is sponsored by Emory University, which has 1,208 total clinical trials registered on ClinicalTrials.gov.
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