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NCT01212744 · ClinicalTrials.gov registry record · Phase 2
Safety, Tolerability, and Efficacy Study of rAvPAL-PEG Administered Daily in Subjects With Phenylketonuria (PKU)
A Phase 2 study, sponsored by BioMarin Pharmaceutical.
- Completed
- Registry status
- Phase 2
- Development phase
- 16
- Enrollment target
NCT01212744: Completed Phase 2 study, sponsored by BioMarin Pharmaceutical.
NCT01212744 is a Phase 2 study that has completed, run by BioMarin Pharmaceutical. The registered enrollment target is 16 participants, below the 133-participant average among 30,622 other Phase 2 trials with a reported enrollment target (88% lower). According to ClinicalTrials.gov, the official US trial registry.
The verdict
NCT01212744, a Phase 2 study, has completed, sponsored by BioMarin Pharmaceutical.
- COMPLETED
- Registry status
- Phase 2
- Development phase
- 16 participants
- Enrollment target
Study Summary
The purpose of this study is to evaluate the effect of daily administration of rAvPAL-PEG on the reduction of blood Phe concentrations in subjects with PKU.
Primary Outcome
Plasma Phe
Interventions
- DRUG rAvPAL-PEG
Trial Details
| Field | Value |
|---|---|
| Enrollment Target | 16 participants |
| Start Date | 2011-03 |
| Est. Completion | 2015-04 |
| Phase | Phase 2 |
What the finished NCT01212744 record still lists
NCT01212744 is an interventional study that assigns participants to a tested intervention. The registry caps enrollment at 16 participants, a relatively small participant target, below the 133-participant average among 30,622 other Phase 2 trials with a reported enrollment target (88% lower).
The record links to 0 conditions, and to 1 intervention - of which rAvPAL-PEG is the first listed.
NCT01212744 does not publish any study locations in the registry export this page uses.
Frequently Asked Questions
What is clinical trial NCT01212744 about?
NCT01212744 is a clinical study titled "Safety, Tolerability, and Efficacy Study of rAvPAL-PEG Administered Daily in Subjects With Phenylketonuria (PKU)". The purpose of this study is to evaluate the effect of daily administration of rAvPAL-PEG on the reduction of blood Phe concentrations in subjects with PKU.
What is the current status of trial NCT01212744?
This trial is currently completed. It is a Phase 2 study. The enrollment target is 16 participants. The study started on 2011-03. Estimated completion is 2015-04.
What interventions are being tested in trial NCT01212744?
The interventions under investigation include: rAvPAL-PEG (DRUG).
Who is sponsoring clinical trial NCT01212744?
This trial is sponsored by BioMarin Pharmaceutical, which has 80 total clinical trials registered on ClinicalTrials.gov.
Learn More About Clinical Trials
How this trial's enrollment target compares
Where NCT01212744's enrollment target sits among peer trials
16 1908th of 2000 higher than 82 of 2,000 other Phase 2 trials
participants (enrollment target), bucketed by value
Each bar is a band; taller bars hold more other Phase 2 trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.
Source ClinicalTrials.gov registry export · 2026-08-08
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