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NCT01163149 · ClinicalTrials.gov registry record · Phase 2

Safety and Efficacy Study of Asfotase Alfa in Adolescents and Adults With Hypophosphatasia (HPP)

A Phase 2 study, sponsored by Alexion Pharmaceuticals.

Completed
Registry status
Phase 2
Development phase
19
Enrollment target

NCT01163149: Completed Phase 2 study, sponsored by Alexion Pharmaceuticals.

NCT01163149 is a Phase 2 study that has completed, run by Alexion Pharmaceuticals. The registered enrollment target is 19 participants, below the 133-participant average among 30,622 other Phase 2 trials with a reported enrollment target (86% lower). According to ClinicalTrials.gov, the official US trial registry.

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The verdict

NCT01163149, a Phase 2 study, has completed, sponsored by Alexion Pharmaceuticals.

COMPLETED
Registry status
Phase 2
Development phase
19 participants
Enrollment target

Study Summary

This clinical trial was conducted to study hypophosphatasia (HPP), a bone disorder caused by gene mutations or changes. These gene mutations cause low levels of an enzyme needed to harden bone. The purpose of this study was to test the safety and efficacy of two doses of the study drug called asfotase alfa as compared to a control group to see effects on adolescents and adults with HPP.

Primary Outcome

Blood samples were collected to evaluate the effect of asfotase alfa on reduction in plasma pyridoxal-5' phosphate (PLP)

Interventions

  • DRUG asfotase alfa

Trial Details

FieldValue
Enrollment Target 19 participants
Start Date 2010-06
Est. Completion 2016-06
Phase Phase 2
Alexion Pharmaceuticals

162 total trials

What the finished NCT01163149 record still lists

NCT01163149 is an interventional study that assigns participants to a tested intervention. The registry caps enrollment at 19 participants, a relatively small participant target, below the 133-participant average among 30,622 other Phase 2 trials with a reported enrollment target (86% lower).

The record links to 0 conditions, and to 1 intervention - of which asfotase alfa is the first listed.

NCT01163149 does not publish any study locations in the registry export this page uses.

Frequently Asked Questions

What is clinical trial NCT01163149 about?

NCT01163149 is a clinical study titled "Safety and Efficacy Study of Asfotase Alfa in Adolescents and Adults With Hypophosphatasia (HPP)". This clinical trial was conducted to study hypophosphatasia (HPP), a bone disorder caused by gene mutations or changes. These gene mutations cause low levels of an enzyme needed to harden bone. The purpose of this study was to test the safety and efficacy of two doses of the study drug called asfota...

What is the current status of trial NCT01163149?

This trial is currently completed. It is a Phase 2 study. The enrollment target is 19 participants. The study started on 2010-06. Estimated completion is 2016-06.

What interventions are being tested in trial NCT01163149?

The interventions under investigation include: asfotase alfa (DRUG).

Who is sponsoring clinical trial NCT01163149?

This trial is sponsored by Alexion Pharmaceuticals, which has 162 total clinical trials registered on ClinicalTrials.gov.

How this trial's enrollment target compares

Where NCT01163149's enrollment target sits among peer trials

19 1894th of 2000 higher than 103 of 2,000 other Phase 2 trials

participants (enrollment target), bucketed by value

Each bar is a band; taller bars hold more other Phase 2 trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.

Source ClinicalTrials.gov registry export · 2026-08-08

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Source: ClinicalTrials.gov NCT01163149, the US trial registry maintained by the National Library of Medicine. NCT01163149 (small enrollment · none site footprint · completed) retrieved and formatted by PlainTrial, see methodology.