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NCT00909363 · ClinicalTrials.gov registry record · Phase 2

Thrombocytopenia and Bleeding in Wiskott-Aldrich Syndrome (WAS) Patients

A Phase 2 study, sponsored by Weill Medical College of Cornell University.

Terminated
Registry status
Phase 2
Development phase
24
Enrollment target

NCT00909363: Clinical Trial Phase 2 study, sponsored by Weill Medical College of Cornell University.

NCT00909363 is a Phase 2 study that was terminated before completion, run by Weill Medical College of Cornell University. The registered enrollment target is 24 participants, below the 133-participant average among 30,622 other Phase 2 trials with a reported enrollment target (82% lower). According to ClinicalTrials.gov, the official US trial registry.

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The verdict

NCT00909363, a Phase 2 study, was terminated before completion, sponsored by Weill Medical College of Cornell University.

TERMINATED
Registry status
Phase 2
Development phase
24 participants
Enrollment target

Study Summary

The purpose of this project is to describe the pathophysiology of thrombocytopenia and bleeding in patients with Wiskott-Aldrich Syndrome (WAS) and determine the response to thrombopoietic agents in vitro and in vivo.

Primary Outcome

number of WAS patients achieving this increase to \> 50,000/uL without rescue medication in the previous 3 weeks during eltrombopag treatment

Interventions

  • DRUG Promacta
  • DIAGNOSTIC_TEST blood drawing in patients with WAS
  • DIAGNOSTIC_TEST blood drawing in healthy controls

Trial Details

FieldValue
Enrollment Target 24 participants
Start Date 2009-06
Est. Completion 2017-06-30
Phase Phase 2

Why NCT00909363 stopped before completion

NCT00909363 is an interventional study that assigns participants to a tested intervention. The registry caps enrollment at 24 participants, a relatively small participant target, below the 133-participant average among 30,622 other Phase 2 trials with a reported enrollment target (82% lower).

The record links to 0 conditions, and to 3 interventions - of which Promacta is the first listed.

NCT00909363 does not publish any study locations in the registry export this page uses.

Frequently Asked Questions

What is clinical trial NCT00909363 about?

NCT00909363 is a clinical study titled "Thrombocytopenia and Bleeding in Wiskott-Aldrich Syndrome (WAS) Patients". The purpose of this project is to describe the pathophysiology of thrombocytopenia and bleeding in patients with Wiskott-Aldrich Syndrome (WAS) and determine the response to thrombopoietic agents in vitro and in vivo.

What is the current status of trial NCT00909363?

This trial is currently terminated. It is a Phase 2 study. The enrollment target is 24 participants. The study started on 2009-06. Estimated completion is 2017-06-30.

What interventions are being tested in trial NCT00909363?

The interventions under investigation include: Promacta (DRUG), blood drawing in patients with WAS (DIAGNOSTIC_TEST), blood drawing in healthy controls (DIAGNOSTIC_TEST).

Who is sponsoring clinical trial NCT00909363?

This trial is sponsored by Weill Medical College of Cornell University, which has 701 total clinical trials registered on ClinicalTrials.gov.

How this trial's enrollment target compares

Where NCT00909363's enrollment target sits among peer trials

24 1756th of 2000 higher than 217 of 2,000 other Phase 2 trials

participants (enrollment target), bucketed by value

Each bar is a band; taller bars hold more other Phase 2 trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.

Source ClinicalTrials.gov registry export · 2026-08-08

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Source: ClinicalTrials.gov NCT00909363, the US trial registry maintained by the National Library of Medicine. NCT00909363 (small enrollment · none site footprint · terminated) retrieved and formatted by PlainTrial, see methodology.