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NCT00351221 · ClinicalTrials.gov registry record · Phase 2

Research Study Using Recombinant Human Insulin-Like Growth Factor-1/Recombinant Human Insulin-Like Growth Factor Binding Protein-3 for Children With Noonan Syndrome

A Phase 2 study, sponsored by Insmed Incorporated.

Terminated
Registry status
Phase 2
Development phase
24
Enrollment target

NCT00351221: Clinical Trial Phase 2 study, sponsored by Insmed Incorporated.

NCT00351221 is a Phase 2 study that was terminated before completion, run by Insmed Incorporated. The registered enrollment target is 24 participants, below the 133-participant average among 30,622 other Phase 2 trials with a reported enrollment target (82% lower). According to ClinicalTrials.gov, the official US trial registry.

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The verdict

NCT00351221, a Phase 2 study, was terminated before completion, sponsored by Insmed Incorporated.

TERMINATED
Registry status
Phase 2
Development phase
24 participants
Enrollment target

Study Summary

The trial will investigate the treatment of growth failure in children with Noonan syndrome. Abnormalities in the growth hormone (GH) - insulin-like growth factor-I (IGF-I) axis resulting in low IGF-I levels have been suggested as a possible cause of short stature seen in Noonan syndrome children. Administration of our investigational product is intended to bypass the abnormalities in the GH-IGF axis, and hopefully improve body growth.

Interventions

  • DRUG rhIGF-1/rhIGFBP-3

Trial Details

FieldValue
Enrollment Target 24 participants
Phase Phase 2
Insmed Incorporated

31 total trials

Why NCT00351221 stopped before completion

NCT00351221 is an interventional study that assigns participants to a tested intervention. The registry caps enrollment at 24 participants, a relatively small participant target, below the 133-participant average among 30,622 other Phase 2 trials with a reported enrollment target (82% lower).

The record links to 0 conditions, and to 1 intervention - of which rhIGF-1/rhIGFBP-3 is the first listed.

NCT00351221 does not publish any study locations in the registry export this page uses.

Frequently Asked Questions

What is clinical trial NCT00351221 about?

NCT00351221 is a clinical study titled "Research Study Using Recombinant Human Insulin-Like Growth Factor-1/Recombinant Human Insulin-Like Growth Factor Binding Protein-3 for Children With Noonan Syndrome". The trial will investigate the treatment of growth failure in children with Noonan syndrome. Abnormalities in the growth hormone (GH) - insulin-like growth factor-I (IGF-I) axis resulting in low IGF-I levels have been suggested as a possible cause of short stature seen in Noonan syndrome children. A...

What is the current status of trial NCT00351221?

This trial is currently terminated. It is a Phase 2 study. The enrollment target is 24 participants.

What interventions are being tested in trial NCT00351221?

The interventions under investigation include: rhIGF-1/rhIGFBP-3 (DRUG).

Who is sponsoring clinical trial NCT00351221?

This trial is sponsored by Insmed Incorporated, which has 31 total clinical trials registered on ClinicalTrials.gov.

How this trial's enrollment target compares

Where NCT00351221's enrollment target sits among peer trials

24 1756th of 2000 higher than 217 of 2,000 other Phase 2 trials

participants (enrollment target), bucketed by value

Each bar is a band; taller bars hold more other Phase 2 trials. The dashed line + filled bar mark this entry. Hover or tap any bar for its full count and share, and where it sits relative to this entry.

Source ClinicalTrials.gov registry export · 2026-08-08

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Source: ClinicalTrials.gov NCT00351221, the US trial registry maintained by the National Library of Medicine. NCT00351221 (small enrollment · none site footprint · terminated) retrieved and formatted by PlainTrial, see methodology.