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NCT00048711 · ClinicalTrials.gov registry record · Phase 2
Open-Label Study of Efficacy and Safety of Recombinant Human N-acetylgalactosamine 4-sulfatase in Patients With MPS VI
A Phase 2 study, sponsored by BioMarin Pharmaceutical.
- Completed
- Registry status
- Phase 2
- Development phase
NCT00048711 is a Phase 2 study that has completed, run by BioMarin Pharmaceutical.
The verdict
NCT00048711, a Phase 2 study, has completed, sponsored by BioMarin Pharmaceutical.
- COMPLETED
- Registry status
- Phase 2
- Development phase
Study Summary
The purpose of the study is evaluate the efficacy, safety, and pharmacokinetics of weekly intravenous infusions of 1 mg/kg recombinant human N-acetylgalactosamine 4-sulfatase (rhASB) in patients diagnosed with Mucopolysaccharidosis VI (MPS VI)
Interventions
- DRUG N-acetylgalactosamine 4-sulfatase
Trial Details
| Field | Value |
|---|---|
| Start Date | 2002-03 |
| Est. Completion | 2006-06 |
| Phase | Phase 2 |
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Full Details on ClinicalTrials.gov ↗What the Registry Record Tells You About NCT00048711
The ClinicalTrials.gov registry entry for NCT00048711 describes a study currently listed as completed, categorized as Phase 2. An enrollment target was not published in the registry record, which is common for early-stage or observational entries. The listed sponsor is BioMarin Pharmaceutical, which has 80 total studies on file at ClinicalTrials.gov.
The record links to 0 conditions, and to 1 intervention - of which N-acetylgalactosamine 4-sulfatase is the first listed.
NCT00048711 reports 0 study locations.
Frequently Asked Questions
What is clinical trial NCT00048711 about?
NCT00048711 is a clinical study titled "Open-Label Study of Efficacy and Safety of Recombinant Human N-acetylgalactosamine 4-sulfatase in Patients With MPS VI". The purpose of the study is evaluate the efficacy, safety, and pharmacokinetics of weekly intravenous infusions of 1 mg/kg recombinant human N-acetylgalactosamine 4-sulfatase (rhASB) in patients diagnosed with Mucopolysaccharidosis VI (MPS VI)
What is the current status of trial NCT00048711?
This trial is currently completed. It is a Phase 2 study. The study started on 2002-03. Estimated completion is 2006-06.
What interventions are being tested in trial NCT00048711?
The interventions under investigation include: N-acetylgalactosamine 4-sulfatase (DRUG).
Who is sponsoring clinical trial NCT00048711?
This trial is sponsored by BioMarin Pharmaceutical, which has 80 total clinical trials registered on ClinicalTrials.gov.
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