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NCT05757310 · ClinicalTrials.gov registry record · Phase 1

A Reduced-Intensity Conditioning Regimen (Cyclophosphamide, Pentostatin, Anti-thymocyte Globulin) Followed by Haploidentical Hematopoietic Stem Cell Transplant for the Treatment of Patients With Refractory or Recurrent Severe Aplastic Anemia

A Phase 1 study of Recurrent Severe Aplastic Anemia and Refractory Severe Aplastic Anemia, sponsored by City of Hope Medical Center.

Recruiting
Registry status
Phase 1
Development phase
6
Enrollment target
1
Study location

NCT05757310 is a Phase 1 study of Recurrent Severe Aplastic Anemia and Refractory Severe Aplastic Anemia that is actively recruiting participants, run by City of Hope Medical Center. The registered enrollment target is 6 participants. The trial reports 1 study location across 1 state.

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The verdict

NCT05757310, a Phase 1 study of Recurrent Severe Aplastic Anemia and Refractory Severe Aplastic Anemia, is actively recruiting participants, sponsored by City of Hope Medical Center.

RECRUITING
Registry status
Phase 1
Development phase
6 participants
Enrollment target
1
Study location

Study Summary

This phase I trial evaluates the safety and feasibility of using a reduced-intensity regimen of cyclophosphamide, pentostatin, and anti-thymocyte globulin prior to a CD4+ T-cell depleted haploidentical hematopoietic cell transplant (haploHCT) for the treatment of patients with severe aplastic anemia that does not respond to treatment (refractory) or that has come back (recurrent). Cyclophosphamide is in a class of medications called alkylating agents. It works by damaging the cell's deoxyribonucleic acid. It may also lower the body's immune response. Pentostatin blocks a protein needed for cell growth. Anti-thymocyte globulin is an immunosuppressive drug can destroy immune cells known as T-cells. HaploHCT transfers blood-forming stem cells from a healthy partially-matched donor to a patient. Administering a regimen of cyclophosphamide, pentostatin, and anti-thymocyte globulin before haploHCT may help make room for the new, healthy cells and may reduce the risk of graft versus host disease.

Interventions

  • DRUG Cyclophosphamide
  • PROCEDURE Biospecimen Collection
  • PROCEDURE Bone Marrow Biopsy
  • BIOLOGICAL Anti-Thymocyte Globulin
  • PROCEDURE Bone Marrow Aspirate

Study Locations (1)

California

  • City of Hope Medical Center - Duarte

Trial Details

FieldValue
Enrollment Target 6 participants
Start Date 2024-11-15
Est. Completion 2027-06-18
Phase Phase 1

Sponsor

City of Hope Medical Center

582 total trials

What the Registry Record Tells You About NCT05757310

The ClinicalTrials.gov registry entry for NCT05757310 describes a study currently listed as recruiting, categorized as Phase 1. The registered enrollment target is 6 participants, a figure that helps gauge the scale of data the investigators plan to collect. The listed sponsor is City of Hope Medical Center, which has 582 total studies on file at ClinicalTrials.gov.

The record links to 2 conditions, with Recurrent Severe Aplastic Anemia appearing as the primary indexed condition, and to 5 interventions - of which Cyclophosphamide is the first listed.

NCT05757310 reports 1 study location spanning 1 distinct geographic area - top geographies include California.

Frequently Asked Questions

What is clinical trial NCT05757310 about?

NCT05757310 is a clinical study titled "A Reduced-Intensity Conditioning Regimen (Cyclophosphamide, Pentostatin, Anti-thymocyte Globulin) Followed by Haploidentical Hematopoietic Stem Cell Transplant for the Treatment of Patients With Refractory or Recurrent Severe Aplastic Anemia". This phase I trial evaluates the safety and feasibility of using a reduced-intensity regimen of cyclophosphamide, pentostatin, and anti-thymocyte globulin prior to a CD4+ T-cell depleted haploidentical hematopoietic cell transplant (haploHCT) for the treatment of patients with severe aplastic anemia...

What is the current status of trial NCT05757310?

This trial is currently recruiting. It is a Phase 1 study. The enrollment target is 6 participants. The study started on 2024-11-15. Estimated completion is 2027-06-18.

What conditions does trial NCT05757310 study?

This clinical trial studies the following conditions: Recurrent Severe Aplastic Anemia, Refractory Severe Aplastic Anemia.

What interventions are being tested in trial NCT05757310?

The interventions under investigation include: Cyclophosphamide (DRUG), Biospecimen Collection (PROCEDURE), Bone Marrow Biopsy (PROCEDURE), Anti-Thymocyte Globulin (BIOLOGICAL), Bone Marrow Aspirate (PROCEDURE).

Who is sponsoring clinical trial NCT05757310?

This trial is sponsored by City of Hope Medical Center, which has 582 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT05757310 being conducted?

This trial has 1 study location across California. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

Data sourced from official public datasets. See our methodology for details. Retrieved and formatted by PlainTrial Editorial

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This page mirrors this trial's own ClinicalTrials.gov registry record, live from the dataset. See our editorial standards & corrections policy, the methodology behind these numbers, or report a data error.