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NCT05095727 · ClinicalTrials.gov registry record · Phase 1

A Study of mRNA-3745 in Adult and Pediatric Participants With Glycogen Storage Disease Type 1a (GSD1a)

A Phase 1 study of Glycogen Storage Disease, sponsored by ModernaTX.

Active
Registry status
Phase 1
Development phase
15
Enrollment target
16
Study locations

NCT05095727 is a Phase 1 study of Glycogen Storage Disease that is active but no longer recruiting, run by ModernaTX. The registered enrollment target is 15 participants, below the 105-participant average among 3 other Glycogen Storage Disease trials with a reported enrollment target (86% lower). The trial reports 16 study locations across 10 states.

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The verdict

NCT05095727, a Phase 1 study of Glycogen Storage Disease, is active but no longer recruiting, sponsored by ModernaTX.

ACTIVE NOT RECRUITING
Registry status
Phase 1
Development phase
15 participants
Enrollment target
16
Study locations

Study Summary

The main goal of this trial is to evaluate the safety and tolerability of mRNA-3745 via intravenous (IV) administration in adult and pediatric participants with GSD1a.

Conditions Studied

Interventions

  • DRUG mRNA-3745

Study Locations (16)

Other

  • AP-HP - Hôpital Antoine Béclère - Clamart
  • CHRU Tours - Hopital Clocheville - Tours
  • Universitair Medisch Centrum Groningen - Groningen
  • Instytut Pomnik Centrum Zdrowia Dziecka - Warsaw
  • Hospital Universitario 12 de Octubre - Madrid
  • Hospital Regional Universitario de Malaga - Málaga

Texas

  • The University of Texas Health Science Center at Houston - Houston
  • Baylor College of Medicine - Houston

Connecticut

  • University of Connecticut Health Center - Farmington

Massachusetts

  • Boston Children's Hospital - Boston

North Carolina

  • Duke University Medical Center - Durham

Ohio

  • Cincinnati Children's Hospital Medical Center - Cincinnati

Pennsylvania

  • Children's Hospital of Philadelphia - Philadelphia

Utah

  • University of Utah - Salt Lake City

Trial Details

FieldValue
Enrollment Target 15 participants
Start Date 2022-06-01
Est. Completion 2026-11-30
Phase Phase 1

Sponsor

ModernaTX

90 total trials

What the Registry Record Tells You About NCT05095727

The ClinicalTrials.gov registry entry for NCT05095727 describes a study currently listed as active not recruiting, categorized as Phase 1. The registered enrollment target is 15 participants, a figure that helps gauge the scale of data the investigators plan to collect, below the 105-participant average among 3 other Glycogen Storage Disease trials with a reported enrollment target (86% lower). The listed sponsor is ModernaTX, which has 90 total studies on file at ClinicalTrials.gov.

The record links to 1 condition, with Glycogen Storage Disease appearing as the primary indexed condition, and to 1 intervention - of which mRNA-3745 is the first listed.

NCT05095727 reports 16 study locations spanning 10 distinct geographic areas - top geographies include Other, Texas, Connecticut.

Frequently Asked Questions

What is clinical trial NCT05095727 about?

NCT05095727 is a clinical study titled "A Study of mRNA-3745 in Adult and Pediatric Participants With Glycogen Storage Disease Type 1a (GSD1a)". The main goal of this trial is to evaluate the safety and tolerability of mRNA-3745 via intravenous (IV) administration in adult and pediatric participants with GSD1a.

What is the current status of trial NCT05095727?

This trial is currently active not recruiting. It is a Phase 1 study. The enrollment target is 15 participants. The study started on 2022-06-01. Estimated completion is 2026-11-30.

What conditions does trial NCT05095727 study?

This clinical trial studies the following conditions: Glycogen Storage Disease.

What interventions are being tested in trial NCT05095727?

The interventions under investigation include: mRNA-3745 (DRUG).

Who is sponsoring clinical trial NCT05095727?

This trial is sponsored by ModernaTX, which has 90 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT05095727 being conducted?

This trial has 16 study locations across Connecticut, Massachusetts, North Carolina, Ohio, Pennsylvania. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

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Data sourced from official public datasets. See our methodology for details. Retrieved and formatted by PlainTrial Editorial

Every figure on PlainTrial is rendered directly from the ClinicalTrials.gov registry, no number is typed in by an editor. This page mirrors this trial's own ClinicalTrials.gov registry record, live from the dataset. See our editorial standards & corrections policy, the methodology behind these numbers, or report a data error.