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NCT04239625 · ClinicalTrials.gov registry record · Phase 2

Open-Label Extension: Tolerability and Effects of ALK-001 on Stargardt Disease (TEASE)

A Phase 2 study of Stargardt Disease and Stargardt Macular Dystrophy, sponsored by Alkeus Pharmaceuticals.

Active
Registry status
Phase 2
Development phase
200
Enrollment target
8
Study locations

NCT04239625 is a Phase 2 study of Stargardt Disease and Stargardt Macular Dystrophy that is active but no longer recruiting, run by Alkeus Pharmaceuticals. The registered enrollment target is 200 participants, above the 79-participant average among 16 other Stargardt Disease trials with a reported enrollment target (153% higher). The trial reports 8 study locations across 8 states.

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The verdict

NCT04239625, a Phase 2 study of Stargardt Disease and Stargardt Macular Dystrophy, is active but no longer recruiting, sponsored by Alkeus Pharmaceuticals.

ACTIVE NOT RECRUITING
Registry status
Phase 2
Development phase
200 participants
Enrollment target
8
Study locations

Study Summary

The purpose of this open-label, multicenter study is to determine the long-term safety, pharmacokinetics and effects of ALK-001 (C20-D3-retinyl acetate) on the progression of Stargardt disease. This study is an extension of NCT02402660 and enrolls participants who are at least 8 years old. Enrollment is by invitation only. Funding Source - FDA OOPD

Interventions

  • DRUG ALK-001

Study Locations (8)

Arizona

  • Alkeus Site - Phoenix

California

  • Alkeus Site - Los Angeles

Colorado

  • Alkeus Site - Aurora

Florida

  • Alkeus Site - Gainesville

Indiana

  • Alkeus Site - Indianapolis

Michigan

  • Alkeus Site - Grand Rapids

New York

  • Alkeus Site - Westbury

Washington

  • Alkeus Site - Silverdale

Trial Details

FieldValue
Enrollment Target 200 participants
Start Date 2019-12-20
Est. Completion 2026-12
Phase Phase 2

Sponsor

Alkeus Pharmaceuticals

3 total trials

What the Registry Record Tells You About NCT04239625

The ClinicalTrials.gov registry entry for NCT04239625 describes a study currently listed as active not recruiting, categorized as Phase 2. The registered enrollment target is 200 participants, a figure that helps gauge the scale of data the investigators plan to collect, above the 79-participant average among 16 other Stargardt Disease trials with a reported enrollment target (153% higher). The listed sponsor is Alkeus Pharmaceuticals, which has 3 total studies on file at ClinicalTrials.gov.

The record links to 4 conditions, with Stargardt Disease appearing as the primary indexed condition, and to 1 intervention - of which ALK-001 is the first listed.

NCT04239625 reports 8 study locations spanning 8 distinct geographic areas - top geographies include Arizona, California, Colorado.

Frequently Asked Questions

What is clinical trial NCT04239625 about?

NCT04239625 is a clinical study titled "Open-Label Extension: Tolerability and Effects of ALK-001 on Stargardt Disease (TEASE)". The purpose of this open-label, multicenter study is to determine the long-term safety, pharmacokinetics and effects of ALK-001 (C20-D3-retinyl acetate) on the progression of Stargardt disease. This study is an extension of NCT02402660 and enrolls participants who are at least 8 years old. Enrollmen...

What is the current status of trial NCT04239625?

This trial is currently active not recruiting. It is a Phase 2 study. The enrollment target is 200 participants. The study started on 2019-12-20. Estimated completion is 2026-12.

What conditions does trial NCT04239625 study?

This clinical trial studies the following conditions: Stargardt Disease, Stargardt Macular Dystrophy, Stargardt Macular Degeneration, Autosomal Recessive Stargardt Disease 1 (ABCA4-related).

What interventions are being tested in trial NCT04239625?

The interventions under investigation include: ALK-001 (DRUG).

Who is sponsoring clinical trial NCT04239625?

This trial is sponsored by Alkeus Pharmaceuticals, which has 3 total clinical trials registered on ClinicalTrials.gov.

Where is trial NCT04239625 being conducted?

This trial has 8 study locations across Arizona, California, Colorado, Florida, Indiana. Contact the study sites directly through ClinicalTrials.gov for enrollment availability.

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Data sourced from official public datasets. See our methodology for details. Retrieved and formatted by PlainTrial Editorial

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